Sibling cases of Duchenne muscular dystrophy with improvement after six months of Viltolarsen

Sibling cases of Duchenne muscular dystrophy with improvement after six months of Viltolarsen
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杜氏肌营养不良症兄弟姐妹接受 Viltolarsen 治疗 6 个月后病情有所改善

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发表时间:
2022
期刊:
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通讯作者:
Akihisa Okumura
Akihisa Okumura
中科院分区:
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文献类型:
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作者:
Hideyuki Iwayama;Kohei Kawahara;Mizuki Takagi;Shingo Numoto;Yoshiteru Azuma;Hirokazu Kurahashi;Yumiko Yasue;Hiroyuki Kawajiri;Atsushi Yanase;Teruyoshi Ito;Shinya Kimura;Toshiyuki Kumagai;Akihisa Okumura

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