Immune responses limit long-term α-galactosidase expression following plasmid-mediated transfer into Fabry mice muscle.

Immune responses limit long-term α-galactosidase expression following plasmid-mediated transfer into Fabry mice muscle.
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在质粒介导的转移到法布里小鼠肌肉中后,免疫反应限制了α-半乳糖苷酶的长期表达。

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期刊:
Mol.Ther. (in press)
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et al.
et al.
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作者:
Pohlschmidt;M.;et al.

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