Response of enthesopathy in ENPP1 deficiency to enzyme replacement therapy in murine models and enthesopathy comorbidities and quality of life in ENPP1-deficient adults.

Response of enthesopathy in ENPP1 deficiency to enzyme replacement therapy in murine models and enthesopathy comorbidities and quality of life in ENPP1-deficient adults.
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ENPP1 缺陷的附着点病对小鼠模型中酶替代疗法的反应以及 ENPP1 缺陷成人的附着点病合并症和生活质量。

DOI:
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发表时间:
2022
期刊:
FASEB journal : official publication of the Federation of American Societies for Experimental Biology
影响因子:
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通讯作者:
Braddock,DemetriosT
Braddock,DemetriosT
中科院分区:
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文献类型:
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作者:
Ansh,AnenyaJ;Nester,Catherine;O'Brien,Christine;Stabach,PaulR;Murtada,Sae-Il;Lester,EthanR;Khursigara,Gus;Molloy,Liz;Carpenter,ThomasO;Ferreira,CarlosR;Braddock,DemetriosT

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