Mutant NADH dehydrogenase subunit 4 gene delivery to mitochondria by targeting sequence-modified adeno-associated virus induces visual loss and optic atrophy in mice.
Mutant NADH dehydrogenase subunit 4 gene delivery to mitochondria by targeting sequence-modified adeno-associated virus induces visual loss and optic atrophy in mice.
复制标题
通过靶向序列修饰的腺相关病毒将突变型 NADH 脱氢酶亚基 4 基因递送至线粒体,可诱导小鼠视力丧失和视神经萎缩。
作者:
Yu,Hong;Ozdemir,SacideS;Koilkonda,RajeshwariD;Chou,Tsung-Han;Porciatti,Vittorio;Chiodo,Vince;Boye,SanfordL;Hauswirth,WilliamW;Lewin,AlfredS;Guy,John