Assessment of Safety and Biodistribution of AAVrh.10hCLN2 Following Intracisternal Administration in Nonhuman Primates for the Treatment of CLN2 Batten Disease.
Assessment of Safety and Biodistribution of AAVrh.10hCLN2 Following Intracisternal Administration in Nonhuman Primates for the Treatment of CLN2 Batten Disease.
复制标题
非人灵长类动物脑池内给药治疗 CLN2 Batten 病后 AAVrh.10hCLN2 的安全性和生物分布评估。
DOI：
10.1089/hum.2023.067
复制
发表时间：
2023
影响因子：
4.2
通讯作者：
Crystal,RonaldG
中科院分区：
文献类型：
--
作者：
De,BishnuP;Rosenberg,JonathanB;Selvan,Nithya;Wilson,Isabelle;Yusufzai,Nadir;Greco,Alessandria;Kaminsky,StephenM;Heier,LindaA;RicartArbona,RodolfoJ;Miranda,IleanaC;Monette,Sebastien;Nair,Anju;Khanna,Richie;Crystal,RonaldG
