CLINICAL TRIAL OF ISOBUTYRAMIDE IN BETA THALASSEMIA AND SICKLE CELL ANEMIA
CLINICAL TRIAL OF ISOBUTYRAMIDE IN BETA THALASSEMIA AND SICKLE CELL ANEMIA
批准号:
3763686
负责人:
DAN COSTIN
金额:
$0.0万
依托单位:
依托单位国家:
美国
项目类别:
财政年份:
--
资助国家:
美国
项目状态:
未结题
起止时间:
至
中文摘要
在这项研究中,异丁酰胺,丁酸的衍生物,将
英文摘要
In this study, isobutyramide, a derivative of butyric acid, will be
investigated to establish the maximally tolerated dose of isobutyramide
and to determine if isobutyramide can stimulate gamma globin synthesis
in patients with beta Thalassemia and sickle cell anemia.
期刊论文(0)
专著(0)
科研奖励(0)
会议论文
BUTYRIC ACID IN THE TREATMENT OF BETA GLOBIN DISEASE
-
批准号:3763716
-
项目类别:
-
资助金额:$0.0万
-
财政年份:--
-
负责人:DAN COSTIN
-
依托单位:
CLINICAL TRIAL OF ISOBUTYRAMIDE IN BETA THALASSEMIA AND SICKLE CELL ANEMIA
-
批准号:3785792
-
项目类别:
-
资助金额:$0.0万
-
财政年份:--
-
负责人:DAN COSTIN
-
依托单位: