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INTRAVENOUS IMMUNE-GLOBULIN THERAPY FOR ADRENOLEUKODYSTROPHY

INTRAVENOUS IMMUNE-GLOBULIN THERAPY FOR ADRENOLEUKODYSTROPHY
肾上腺脑白质营养不良的静脉注射免疫球蛋白治疗
批准号:
3863284
负责人:
WILLIAM R RIZZO
金额:
$0.0万
依托单位国家:
美国
项目类别:
财政年份:
--
资助国家:
美国
项目状态:
未结题
起止时间:

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中文摘要
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英文摘要
To determine if symptomatic patients with ALD have altered immunological systems or show evidence of autoimmune response in the brain to determine if immunological response of the patient or neurological symptoms of ALD are mitigated by administration of intravenous immune-globulin.
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FATTY ACID METABOLISM IN ADRENOLEUKODYSTROPHY--EURIC ACID THERAPY
FATTY ALCOHOL METABOLISM IN SJOGREN-LARSSON SYNDROME
ERUCIC ACID THERAPY/PRESYMPTOMATIC ADRENOLEUKODYSTROPHY
FATTY ACID METABOLISM IN ADRENOLEUKODYSTROPHY AND ADRENOMYELONEUROPATHY