CLINICAL TRIAL: SAPROPTERIN EXPANDED ACCESS PROGRAM (SEAP)
CLINICAL TRIAL: SAPROPTERIN EXPANDED ACCESS PROGRAM (SEAP)
批准号:
7724974
负责人:
WILLIAM L. NYHAN
金额:
$0.18万
依托单位国家:
美国
项目类别:
财政年份:
2007
资助国家:
美国
项目状态:
已结题
起止时间:
2007-12-01 至 2008-11-30
中文摘要
这个子项目是许多研究子项目中利用
资源由NIH/NCRR资助的中心拨款提供。子项目和
调查员(PI)可能从NIH的另一个来源获得了主要资金,
并因此可以在其他清晰的条目中表示。列出的机构是
该中心不一定是调查人员的机构。
为苯丙酮尿症(PKU)所致的高苯丙氨酸血症(HPA)患者提供盐酸腐普特林,并在扩大准入计划(EAP)中收集有关该药物安全性的更多信息,直到商业化产品上市。
英文摘要
This subproject is one of many research subprojects utilizing the
resources provided by a Center grant funded by NIH/NCRR. The subproject and
investigator (PI) may have received primary funding from another NIH source,
and thus could be represented in other CRISP entries. The institution listed is
for the Center, which is not necessarily the institution for the investigator.
To provide patients with hyperphenylalaninemia (HPA) due to Phenylketonuria (PKU) access to sapropterin dihydrochloride and to collect more information about the safety of the drug in an expanded access program (EAP) until commercial product is available.
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会议论文
AMINO ACID INTERRELATIONSHIPS IN HUMAN METABOLIC DISEASE: INBORN ERRORS
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批准号:8166776
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项目类别:
-
资助金额:$0.03万
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财政年份:2009
-
负责人:WILLIAM L. NYHAN
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依托单位:
AMINO ACID INTERRELATIONSHIPS IN HUMAN METABOLIC DISEASE: INBORN ERRORS
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批准号:7950905
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项目类别:
-
资助金额:$0.23万
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财政年份:2008
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负责人:WILLIAM L. NYHAN
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依托单位:
DISORDERS OF FAT METABOLISM
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批准号:7950907
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项目类别:
-
资助金额:$0.11万
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财政年份:2008
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负责人:WILLIAM L. NYHAN
-
依托单位:
LESCH-NYHAN SYNDROME AND RELATED METABOLIC DISORDERS
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批准号:7950904
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项目类别:
-
资助金额:$0.11万
-
财政年份:2008
-
负责人:WILLIAM L. NYHAN
-
依托单位:
AMINO ACID INTERRELATIONSHIPS IN HUMAN METABOLIC DISEASE: INBORN ERRORS
-
批准号:7724869
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项目类别:
-
资助金额:$0.27万
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财政年份:2007
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负责人:WILLIAM L. NYHAN
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依托单位:
LESCH-NYHAN SYNDROME AND RELATED METABOLIC DISORDERS
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批准号:7606489
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项目类别:
-
资助金额:$0.12万
-
财政年份:2006
-
负责人:WILLIAM L. NYHAN
-
依托单位:
AMINO ACID INTERRELATIONSHIPS IN HUMAN METABOLIC DISEASE: INBORN ERRORS
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批准号:7606490
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项目类别:
-
资助金额:$0.23万
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财政年份:2006
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负责人:WILLIAM L. NYHAN
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依托单位:
LESCH-NYHAN SYNDROME AND RELATED DISORDERS OF PURINE METABOLISM
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批准号:7374122
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项目类别:
-
资助金额:$0.11万
-
财政年份:2006
-
负责人:WILLIAM L. NYHAN
-
依托单位:
AMINO ACID INTERRELATIONSHIPS IN HUMAN METABOLIC DISEASE: INBORN ERRORS
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批准号:7374123
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项目类别:
-
资助金额:$1.05万
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财政年份:2006
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负责人:WILLIAM L. NYHAN
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依托单位:
Amino Acid Interrelationships in Human Metabolic Disease: Inborn Errors
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批准号:7045361
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项目类别:
-
资助金额:$2.6万
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财政年份:2003
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负责人:WILLIAM L. NYHAN
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依托单位:
Disorders of Fat Metabolism
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批准号:7045363
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项目类别:
-
资助金额:$0.06万
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财政年份:2003
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负责人:WILLIAM L. NYHAN
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依托单位:
Effect of Alanine Ingestion on Exercise Performance
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批准号:7045455
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项目类别:
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资助金额:$1.71万
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财政年份:2003
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负责人:WILLIAM L. NYHAN
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依托单位:
Lesch-Nyhan Syndrome--Related Disorders of Purine Metab
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批准号:7045360
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项目类别:
-
资助金额:$0.08万
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财政年份:2003
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负责人:WILLIAM L. NYHAN
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依托单位:
Dichloroacetate in the Treatment of Congenital Lactic Acidemia
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批准号:7045389
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项目类别:
-
资助金额:$0.59万
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财政年份:2003
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负责人:WILLIAM L. NYHAN
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依托单位:
DISORDERS OF FAT METABOLISM
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批准号:7205543
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项目类别:
-
资助金额:$0.06万
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财政年份:2003
-
负责人:WILLIAM L. NYHAN
-
依托单位:
AMINO ACID INTERRELATIONSHIPS IN HUMAN METABOLIC DISEASE: INBORN ERRORS
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批准号:7205541
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项目类别:
-
资助金额:$1.71万
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财政年份:2003
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负责人:WILLIAM L. NYHAN
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依托单位:
DISORDERS OF FAT METABOLISM
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批准号:6117886
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项目类别:
-
资助金额:$1.46万
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财政年份:1998
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负责人:WILLIAM L. NYHAN
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依托单位:
AMINO ACID INTERRELATIONSHIPS IN METABOLIC DISEASE--INBORN ERRORS
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批准号:6117883
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项目类别:
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资助金额:$1.46万
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财政年份:1998
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负责人:WILLIAM L. NYHAN
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依托单位:
DISORDERS OF FAT METABOLISM
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批准号:6249056
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项目类别:
-
资助金额:$1.64万
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财政年份:1997
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负责人:WILLIAM L. NYHAN
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依托单位:
DISORDERS OF FAT METABOLISM
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批准号:6279081
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项目类别:
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资助金额:$1.43万
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财政年份:1997
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负责人:WILLIAM L. NYHAN
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依托单位: