课题基金 / 基金详情

CLINICAL TRIAL: SAPROPTERIN EXPANDED ACCESS PROGRAM (SEAP)

CLINICAL TRIAL: SAPROPTERIN EXPANDED ACCESS PROGRAM (SEAP)
临床试验:SAPPROTERIN 扩展获取计划 (SEAP)
批准号:
7724974
负责人:
WILLIAM L. NYHAN
金额:
$0.18万
依托单位国家:
美国
项目类别:
财政年份:
2007
资助国家:
美国
项目状态:
已结题
起止时间:
2007-12-01 至 2008-11-30

项目摘要

项目成果

WILLIAM L. NYHAN的其他基金

相关文献

中文摘要
翻译
这个子项目是众多研究子项目之一
英文摘要
This subproject is one of many research subprojects utilizing the resources provided by a Center grant funded by NIH/NCRR. The subproject and investigator (PI) may have received primary funding from another NIH source, and thus could be represented in other CRISP entries. The institution listed is for the Center, which is not necessarily the institution for the investigator. To provide patients with hyperphenylalaninemia (HPA) due to Phenylketonuria (PKU) access to sapropterin dihydrochloride and to collect more information about the safety of the drug in an expanded access program (EAP) until commercial product is available.
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会议论文
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