课题基金 / 基金详情

CLINICAL TRIAL: SAPROPTERIN EXPANDED ACCESS PROGRAM (SEAP)

CLINICAL TRIAL: SAPROPTERIN EXPANDED ACCESS PROGRAM (SEAP)
临床试验：SAPPROTERIN 扩展获取计划 (SEAP)
批准号：
7724974
负责人：
WILLIAM L. NYHAN
金额：
$0.18万
依托单位：
UNIVERSITY OF CALIFORNIA, SAN DIEGO
依托单位国家：
美国
项目类别：
财政年份：
2007
资助国家：
美国
项目状态：
已结题
起止时间：
2007-12-01 至 2008-11-30
来源：
https://reporter.nih.gov/project-details/7724974
关键词：
Clinical TrialsComputer Retrieval of Information on Scientific Projects DatabaseFundingGrantHyperphenylalaninaemiasInstitutionPatientsPharmaceutical PreparationsResearchResearch PersonnelResourcesSafetySourceUnited States National Institutes of Healthprograms

项目摘要

项目成果

WILLIAM L. NYHAN的其他基金

相关文献

中文摘要
翻译
这个子项目是许多研究子项目中利用 资源由NIH/NCRR资助的中心拨款提供。子项目和 调查员(PI)可能从NIH的另一个来源获得了主要资金， 并因此可以在其他清晰的条目中表示。列出的机构是 该中心不一定是调查人员的机构。 为苯丙酮尿症(PKU)所致的高苯丙氨酸血症(HPA)患者提供盐酸腐普特林，并在扩大准入计划(EAP)中收集有关该药物安全性的更多信息，直到商业化产品上市。
英文摘要
This subproject is one of many research subprojects utilizing the resources provided by a Center grant funded by NIH/NCRR. The subproject and investigator (PI) may have received primary funding from another NIH source, and thus could be represented in other CRISP entries. The institution listed is for the Center, which is not necessarily the institution for the investigator. To provide patients with hyperphenylalaninemia (HPA) due to Phenylketonuria (PKU) access to sapropterin dihydrochloride and to collect more information about the safety of the drug in an expanded access program (EAP) until commercial product is available.
期刊论文(0)
专著(0)
科研奖励(0)
会议论文
AMINO ACID INTERRELATIONSHIPS IN HUMAN METABOLIC DISEASE: INBORN ERRORS
AMINO ACID INTERRELATIONSHIPS IN HUMAN METABOLIC DISEASE: INBORN ERRORS
DISORDERS OF FAT METABOLISM
LESCH-NYHAN SYNDROME AND RELATED METABOLIC DISORDERS