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Getting Ready for Vision Therapy in Peroxisome Biogenesis Disorders

Getting Ready for Vision Therapy in Peroxisome Biogenesis Disorders
为过氧化物酶体生物发生障碍的视觉治疗做好准备
批准号：
357916
负责人：
Braverman Nancy E
金额：
$69.89万
依托单位：
Research Institute of the McGill University Health Centre
依托单位国家：
加拿大
项目类别：
Operating Grants
财政年份：
2016
资助国家：
加拿大
项目状态：
已结题
起止时间：
2016-10-01 至 2021-10-01
来源：
https://webapps.cihr-irsc.gc.ca/decisions/p/project_details.html?applId=357916&lang=en
关键词：
Clinical Trial Endpoints Drug Treatment Mouse Models Natural History Studies Orphan Diseases Peroxisome Diseases Peroxisome Metabolic Pathways Retinal Degeneration

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中文摘要
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英文摘要
Our goal is to identify therapies for a group of genetic diseases, the Peroxisome Biogenesis Disorders (PBD). Progressive retinal degeneration leading to blindness is one of the major, untreatable handicaps in this condition and correcting vision would va
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