GENE REPLACEMENT THERAPY
GENE REPLACEMENT THERAPY
批准号:
2142469
负责人:
C THOMAS CASKEY
金额:
$31.44万
依托单位国家:
美国
项目类别:
财政年份:
1990
资助国家:
美国
项目状态:
已结题
起止时间:
1990-08-01 至 1997-07-31
期刊论文(6)
专著(0)
科研奖励(0)
会议论文
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Gene therapy in man and mice: adenosine deaminase deficiency, ornithine transcarbamylase deficiency, and Duchenne muscular dystrophy.
人和小鼠的基因治疗:腺苷脱氨酶缺乏症、鸟氨酸转氨甲酰酶缺乏症和杜氏肌营养不良症。
DOI:
10.1007/978-1-4615-7703-4_12
发表时间:
1991
期刊:
Advances in experimental medicine and biology
影响因子:
--
作者:
[Grompe,M, Mitani,K, Lee,CC, Jones,SN, Caskey,CT]
通讯作者:
Caskey,CT
Gene transfer of adenosine deaminase into primitive human hematopoietic progenitor cells.
将腺苷脱氨酶基因转移到原始人类造血祖细胞中。
DOI:
10.1089/hum.1991.2.3-203
发表时间:
1991
期刊:
Human gene therapy
影响因子:
4.2
作者:
[Cournoyer,D, Scarpa,M, Mitani,K, Moore,KA, Markowitz,D, Bank,A, Belmont,JW, Caskey,CT]
通讯作者:
Caskey,CT
Evaluation of lymphoid-specific enhancer addition or substitution in a basic retrovirus vector.
评估基本逆转录病毒载体中淋巴特异性增强子的添加或替换。
DOI:
10.1089/hum.1991.2.4-307
发表时间:
1991
期刊:
Human gene therapy
影响因子:
4.2
作者:
[Moore,KA, Scarpa,M, Kooyer,S, Utter,A, Caskey,CT, Belmont,JW]
通讯作者:
Belmont,JW
Gene transfer therapy for heritable disease: cell and expression targeting.
遗传性疾病的基因转移疗法:细胞和表达靶向。
DOI:
10.1098/rstb.1993.0019
发表时间:
1993
期刊:
Philosophical transactions of the Royal Society of London. Series B, Biological sciences
影响因子:
--
作者:
[Mitani,K, Clemens,PR, Moseley,AB, Caskey,CT]
通讯作者:
Caskey,CT
IDENTIFICATION FO SUBSTRATES FOR MYOTONIN KINASE IN MYOTONIC DYSTROPHY
-
批准号:6110446
-
项目类别:
-
资助金额:$17.16万
-
财政年份:1999
-
负责人:C THOMAS CASKEY
-
依托单位:
IDENTIFICATION FO SUBSTRATES FOR MYOTONIN KINASE IN MYOTONIC DYSTROPHY
-
批准号:6273030
-
项目类别:
-
资助金额:$16.69万
-
财政年份:1998
-
负责人:C THOMAS CASKEY
-
依托单位:
IDENTIFICATION FO SUBSTRATES FOR MYOTONIN KINASE IN MYOTONIC DYSTROPHY
-
批准号:6242440
-
项目类别:
-
资助金额:$15.88万
-
财政年份:1997
-
负责人:C THOMAS CASKEY
-
依托单位:
IN VIVO GENE DELIVERY FOR LONG-TERM EXPRESSION
-
批准号:6110296
-
项目类别:
-
资助金额:$0.0万
-
财政年份:1997
-
负责人:C THOMAS CASKEY
-
依托单位:
GENOME SEQUENCING AND ANALYSIS CONFERENCE IV
-
批准号:3435538
-
项目类别:
-
资助金额:$2.91万
-
财政年份:1992
-
负责人:C THOMAS CASKEY
-
依托单位:
AUTOMATED DNA SEQUENCING SYSTEM
-
批准号:3521105
-
项目类别:
-
资助金额:$18.2万
-
财政年份:1991
-
负责人:C THOMAS CASKEY
-
依托单位:
HUMAN GENOME PROGRAM CENTER
-
批准号:3103200
-
项目类别:
-
资助金额:$6.19万
-
财政年份:1991
-
负责人:C THOMAS CASKEY
-
依托单位:
BCM HUMAN GENOME PROGRAM CENTER
-
批准号:3103202
-
项目类别:
-
资助金额:$183.61万
-
财政年份:1991
-
负责人:C THOMAS CASKEY
-
依托单位:
CHROMOSOME 17P YAC'S
-
批准号:3103198
-
项目类别:
-
资助金额:$12.63万
-
财政年份:1991
-
负责人:C THOMAS CASKEY
-
依托单位:
BCM HUMAN GENOME PROGRAM CENTER
-
批准号:3103197
-
项目类别:
-
资助金额:$198.36万
-
财政年份:1991
-
负责人:C THOMAS CASKEY
-
依托单位:
BCM HUMAN GENOME PROGRAM CENTER
-
批准号:3103201
-
项目类别:
-
资助金额:$181.56万
-
财政年份:1991
-
负责人:C THOMAS CASKEY
-
依托单位:
GENE REPLACEMENT THERAPY--HUMAN AND MOUSE MODELS
-
批准号:3243866
-
项目类别:
-
资助金额:$27.48万
-
财政年份:1990
-
负责人:C THOMAS CASKEY
-
依托单位:
GENE REPLACEMENT THERAPY--HUMAN AND MOUSE MODELS
-
批准号:3243867
-
项目类别:
-
资助金额:$0.71万
-
财政年份:1990
-
负责人:C THOMAS CASKEY
-
依托单位:
GENE REPLACEMENT THERAPY--HUMAN AND MOUSE MODELS
-
批准号:3243868
-
项目类别:
-
资助金额:$27.48万
-
财政年份:1990
-
负责人:C THOMAS CASKEY
-
依托单位:
GENE REPLACEMENT THERAPY--HUMAN AND MOUSE MODELS
-
批准号:3243869
-
项目类别:
-
资助金额:$28.88万
-
财政年份:1990
-
负责人:C THOMAS CASKEY
-
依托单位:
GENE REPLACEMENT THERAPY--HUMAN AND MOUSE MODELS
-
批准号:3243870
-
项目类别:
-
资助金额:$30.13万
-
财政年份:1990
-
负责人:C THOMAS CASKEY
-
依托单位:
X CHROMOSOME CLONING WORKSHOP
-
批准号:3435499
-
项目类别:
-
资助金额:$2.72万
-
财政年份:1989
-
负责人:C THOMAS CASKEY
-
依托单位:
LARGE INSERT CLONING WORKSHOP
-
批准号:3435498
-
项目类别:
-
资助金额:$3.32万
-
财政年份:1989
-
负责人:C THOMAS CASKEY
-
依托单位:
X CHROMOSOME CLONING WORKSHOP
-
批准号:3566199
-
项目类别:
-
资助金额:$2.72万
-
财政年份:1989
-
负责人:C THOMAS CASKEY
-
依托单位:
LARGE INSERT CLONING WORKSHOP
-
批准号:3566200
-
项目类别:
-
资助金额:$3.32万
-
财政年份:1989
-
负责人:C THOMAS CASKEY
-
依托单位:
海外基金