TREATING SCID DUE TO ADA DEFICIENCY WITH CD34+ SELECTED AUTOLOGOUS STEM CELLS
TREATING SCID DUE TO ADA DEFICIENCY WITH CD34+ SELECTED AUTOLOGOUS STEM CELLS
批准号:
6280790
负责人:
Diane W. Wara
金额:
$2.39万
依托单位国家:
美国
项目类别:
财政年份:
1997
资助国家:
美国
项目状态:
已结题
起止时间:
1997-12-01 至 1998-11-30
关键词:
CD34 molecule adenosine deaminase autologous transplantation cell transplantation clinical research enzyme deficiency gene therapy genetic transduction hematopoietic stem cells hematopoietic tissue transplantation human genetic material tag human subject human therapy evaluation newborn human (0-6 weeks) severe combined immunodeficiency
中文摘要
点击翻译按钮获取中文摘要
英文摘要
This is a study to investigate the treatment of severe combined
immunodeficiency (SCID) due to adenosine deaminase deficiency (ADA-) with
CD34+ selected autologous hematopoietic stem cells transduced with a human
ADA gene in a newborn.
期刊论文(0)
专著(0)
科研奖励(0)
会议论文
PACTG P1030: PHASE I/II STUDY OF LOPINAVIR/RITONAVIR IN HIV-1 INFECTED INFANTS
-
批准号:7204875
-
项目类别:
-
资助金额:$1.25万
-
财政年份:2005
-
负责人:Diane W. Wara
-
依托单位:
PACTG P1045: MORPHOLOGIC AND METABOLIC ABNORMALITIES IN CHILDREN & YOUTH
-
批准号:7204900
-
项目类别:
-
资助金额:$0.83万
-
财政年份:2005
-
负责人:Diane W. Wara
-
依托单位:
PEDIATRIC LATE OUTCOMES PROTOCOL (AIDS CLINICAL TRIALS GROUP: 219C)
-
批准号:7204914
-
项目类别:
-
资助金额:$48.12万
-
财政年份:2005
-
负责人:Diane W. Wara
-
依托单位:
CLINICAL AND MOLECULAR INVESTIGATION OF PRIMARY IMMUNODEFICIENCIES
-
批准号:7204913
-
项目类别:
-
资助金额:$28.26万
-
财政年份:2005
-
负责人:Diane W. Wara
-
依托单位:
EFFECTS OF HAART ON THE RECOVERY OF IMMUNE FUNCTION IN HIV-INFECTED CHILDREN
-
批准号:7204838
-
项目类别:
-
资助金额:$0.83万
-
财政年份:2005
-
负责人:Diane W. Wara
-
依托单位:
PACTG P1057: PHASE I/II RANDOMIZED TRIAL OF COLD ADAPTED INFLUENZA VACCINE
-
批准号:7204907
-
项目类别:
-
资助金额:$1.53万
-
财政年份:2005
-
负责人:Diane W. Wara
-
依托单位:
PACTG P1042S: COGNITIVE, BEHAVIORAL AND PSYCHOSOCIAL CORRELATES
-
批准号:7204910
-
项目类别:
-
资助金额:$0.28万
-
财政年份:2005
-
负责人:Diane W. Wara
-
依托单位:
PHASE I/II STUDY OF ALVAC HIV VACCINE IN CHILDREN
-
批准号:7204833
-
项目类别:
-
资助金额:$0.28万
-
财政年份:2005
-
负责人:Diane W. Wara
-
依托单位:
PACTG P1026S:PHARMACOKINETIC PROPERTIES OF ANTIRETROVIRAL DRUGS DURING PREGNANCY
-
批准号:7204884
-
项目类别:
-
资助金额:$0.42万
-
财政年份:2005
-
负责人:Diane W. Wara
-
依托单位:
DEFECTIVE T- AND B- CELL SIGNALING IN PATIENTS WITH INHERITED IMMUNODEFICIENCIES
-
批准号:7204840
-
项目类别:
-
资助金额:$13.21万
-
财政年份:2005
-
负责人:Diane W. Wara
-
依托单位:
PACTG 1020-A, VERSION 20
-
批准号:7204847
-
项目类别:
-
资助金额:$12.06万
-
财政年份:2005
-
负责人:Diane W. Wara
-
依托单位:
PACTG P1024: EVALUATION OF PNEUMOCOCCAL VACCINE IN HIV-INFECTED CHILDREN
-
批准号:7204861
-
项目类别:
-
资助金额:$0.28万
-
财政年份:2005
-
负责人:Diane W. Wara
-
依托单位:
PACTG P1025: PERINATAL CORE PROTOCOL FOR DATA FROM HIV-INFECTED PREGNANT WOMEN
-
批准号:7204872
-
项目类别:
-
资助金额:$6.79万
-
财政年份:2005
-
负责人:Diane W. Wara
-
依托单位:
Phase I/II trial of subcutaneous IL-2 with antiretroviral therapy in HIV
-
批准号:7043543
-
项目类别:
-
资助金额:$14.66万
-
财政年份:2004
-
负责人:Diane W. Wara
-
依托单位:
PACTG P1025: Perinatal core protocol for data from HIV-infected pregnant women
-
批准号:7043578
-
项目类别:
-
资助金额:$9.52万
-
财政年份:2004
-
负责人:Diane W. Wara
-
依托单位:
PACTG P1026S:PHARMACOKINETIC PROPERTIES OF ANTIRETROVIRAL DRUGS DURING PREGNANCY
-
批准号:7043590
-
项目类别:
-
资助金额:$0.43万
-
财政年份:2004
-
负责人:Diane W. Wara
-
依托单位:
CLINICAL AND MOLECULAR INVESTIGATION OF PRIMARY IMMUNODEFICIENCIES
-
批准号:7043596
-
项目类别:
-
资助金额:$22.93万
-
财政年份:2004
-
负责人:Diane W. Wara
-
依托单位:
Defective T- and B- cell signaling in patients with inherited immunodeficiencies
-
批准号:7043540
-
项目类别:
-
资助金额:$12.58万
-
财政年份:2004
-
负责人:Diane W. Wara
-
依托单位:
Immunological and neurodevelopmental consequences of chromosome 22q11.2 deletion
-
批准号:7043530
-
项目类别:
-
资助金额:$0.16万
-
财政年份:2004
-
负责人:Diane W. Wara
-
依托单位:
Phase I/II study of ALVAC HIV vaccine in children
-
批准号:7043532
-
项目类别:
-
资助金额:$0.54万
-
财政年份:2004
-
负责人:Diane W. Wara
-
依托单位:
海外基金