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TREATING SCID DUE TO ADA DEFICIENCY WITH CD34+ SELECTED AUTOLOGOUS STEM CELLS

TREATING SCID DUE TO ADA DEFICIENCY WITH CD34+ SELECTED AUTOLOGOUS STEM CELLS
使用 CD34 精选自体干细胞治疗因 ADA 缺乏所致的 SCID
批准号:
6280790
负责人:
Diane W. Wara
金额:
$2.39万
依托单位国家:
美国
项目类别:
财政年份:
1997
资助国家:
美国
项目状态:
已结题
起止时间:
1997-12-01 至 1998-11-30

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中文摘要
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英文摘要
This is a study to investigate the treatment of severe combined immunodeficiency (SCID) due to adenosine deaminase deficiency (ADA-) with CD34+ selected autologous hematopoietic stem cells transduced with a human ADA gene in a newborn.
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