EXPANDED ACCESS USE OF MYOZYME (ALGLUCOSDASE ALFA) IN PATIENTS WITH INFANTILE-ON

扩大 MYOZYME（葡萄糖苷酶 ALFA）在 INFANTILE-ON 患者中的使用范围

• 批准号: 7380775
• 负责人: LESLIE B SMOOT
• 金额: $ 0.44万
• 依托单位: BOSTON CHILDREN'S HOSPITAL
• 依托单位国家: 美国
• 财政年份: 2006
• 资助国家: 美国
• 起止时间: 2006-04-01 至 2007-03-31
• 项目状态: 已结题
• 来源: https://reporter.nih.gov/project-details/7380775
• 关键词: EXPANDED; ACCESS; USE; MYOZYME; ALGLUCOSDASE

This subproject is one of many research subprojects utilizing the resources provided by a Center grant funded by NIH/NCRR. The subproject and investigator (PI) may have received primary funding from another NIH source, and thus could be represented in other CRISP entries. The institution listed is for the Center, which is not necessarily the institution for the investigator. This research study being conducted to evaluate the long term safety and potential effectiveness of Myozyme as a potential therapy for Pompe dise

该子项目是利用 NIH/NCRR 资助的中心拨款提供的资源的众多研究子项目之一。子项目和研究者 (PI) 可能已从另一个 NIH 来源获得主要资金，因此可以在其他 CRISP 条目中得到体现。列出的机构是中心的机构，不一定是研究者的机构。这项研究旨在评估 Myozyme 作为庞贝氏症潜在疗法的长期安全性和潜在有效性