MYOZYME (ALGLUCOSDASE ALFA) IN POMPE DISEASE

MYOZYME（葡萄糖苷酶 ALFA）在庞贝病中的应用

• 批准号: 7607289
• 负责人: LESLIE B SMOOT
• 金额: $ 0.29万
• 依托单位: BOSTON CHILDREN'S HOSPITAL
• 依托单位国家: 美国
• 财政年份: 2007
• 资助国家: 美国
• 起止时间: 2007-04-01 至 2008-03-31
• 项目状态: 已结题
• 来源: https://reporter.nih.gov/project-details/7607289
• 关键词: Computer Retrieval of Information on Scientific Projects Database; Effectiveness; Funding; Glycogen storage disease type II; Grant; Institution; Research; Research Personnel; Resources; Safety; Source; United States National Institutes of Health; research study

This subproject is one of many research subprojects utilizing the resources provided by a Center grant funded by NIH/NCRR. The subproject and investigator (PI) may have received primary funding from another NIH source, and thus could be represented in other CRISP entries. The institution listed is for the Center, which is not necessarily the institution for the investigator. This research study being conducted to evaluate the long term safety and potential effectiveness of Myozyme as a potential therapy for Pompe disease.

这个子项目是许多研究子项目中的一个 由NIH/NCRR资助的中心赠款提供的资源。子项目和 研究者（PI）可能从另一个NIH来源获得了主要资金， 因此可以在其他CRISP条目中表示。所列机构为 研究中心，而研究中心不一定是研究者所在的机构。 本研究旨在评价美而赞作为庞贝氏症潜在治疗方法的长期安全性和潜在有效性。