MYOZYME (ALGLUCOSDASE ALFA) IN POMPE DISEASE

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This subproject is one of many research subprojects utilizing the resources provided by a Center grant funded by NIH/NCRR. The subproject and investigator (PI) may have received primary funding from another NIH source, and thus could be represented in other CRISP entries. The institution listed is for the Center, which is not necessarily the institution for the investigator. This research study being conducted to evaluate the long term safety and potential effectiveness of Myozyme as a potential therapy for Pompe disease.