CLINICAL TRIAL: INVESTIGATE THE EFFICACY & SAFETY OF PURIFIED C1 ESTERASE INHIBI

临床试验:研究疗效

基本信息

  • 批准号:
    7724937
  • 负责人:
  • 金额:
    $ 0.23万
  • 依托单位:
  • 依托单位国家:
    美国
  • 项目类别:
  • 财政年份:
    2007
  • 资助国家:
    美国
  • 起止时间:
    2007-12-01 至 2008-11-30
  • 项目状态:
    已结题

项目摘要

This subproject is one of many research subprojects utilizing the resources provided by a Center grant funded by NIH/NCRR. The subproject and investigator (PI) may have received primary funding from another NIH source, and thus could be represented in other CRISP entries. The institution listed is for the Center, which is not necessarily the institution for the investigator. Determine whether C1INH-nf treated subjects have shorter median time to relief of the defining symptoms compared to placebo. Test whether time to relief is different in subjects treated with C1INH-nr compared to placebo.
这个子项目是许多研究子项目中的一个 由NIH/NCRR资助的中心赠款提供的资源。子项目和 研究者(PI)可能从另一个NIH来源获得了主要资金, 因此可以在其他CRISP条目中表示。所列机构为 研究中心,而研究中心不一定是研究者所在的机构。 确定与安慰剂相比,C1 INH-nf治疗受试者至定义症状缓解的中位时间是否更短。 检验接受C1 INH-nr治疗的受试者与接受安慰剂治疗的受试者相比,至缓解时间是否存在差异。

项目成果

期刊论文数量(0)
专著数量(0)
科研奖励数量(0)
会议论文数量(0)
专利数量(0)

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Bruce L. Zuraw其他文献

A Comprehensive Approach to Assessing the Value of Prophylactic Therapy for the Ultra Rare Disease Hereditary Angioedema Using Real World Patient Data
  • DOI:
    10.1016/j.jaci.2018.12.960
  • 发表时间:
    2019-02-01
  • 期刊:
  • 影响因子:
  • 作者:
    Anthony J. Castaldo;Christian Jervelund;Andreas R. Kirk;Deborah Corcoran;Henrik Balle Boysen;Janet F. Long;Sandra C. Christiansen;Bruce L. Zuraw
  • 通讯作者:
    Bruce L. Zuraw
Abstracts from the 10th C1-inhibitor deficiency workshop
  • DOI:
    10.1186/s13223-017-0198-5
  • 发表时间:
    2017-06-15
  • 期刊:
  • 影响因子:
    2.400
  • 作者:
    Alvin H. Schmaier;Marco Cicardi;Avner Reshef;Dumitru Moldovan;Attila Mócsai;Margarita López-Trascasa;Alberto López Lera;Nancy J. Brown;Anastasios E. Germenis;Rafael Filippelli-Silva;Diego A. Duarte;Renan P. Martin;Camila L. Veronez;Michel Bouvier;Michael Bader;Claudio M. Costa-Neto;João Bosco Pesquero;Xavier Charest-Morin;François Marceau;Georges-É. Rivard;Arnaud Bonnefoy;Éric Wagner;Márta L. Debreczeni;Zsuzsanna Németh;Erika Kajdácsi;Endre Schwaner;László Cervenak;Gábor Oroszlán;András Szilágyi;Ráhel Dani;Péter Závodszky;Péter Gál;József Dobó;Jacques Hébert;Matthieu Vincent;Jean-Nicolas Boursiquot;Hugo Chapdeleine;Marylin Desjardins;Benoit Laramée;Rémi Gagnon;Nancy Payette;Oleksandra Lepeshkina;Delphine Charignon;Arije Ghannam;Denise Ponard;Christian Drouet;Kusumam Joseph;Baby G. Tholanikunnel;Daniel J. Sexton;Allen P. Kaplan;Stefania Loffredo;Maria Bova;Anne Lise Ferrara;Angelica Petraroli;Chiara Suffritti;Nóra Veszeli;Andrea Zanichelli;Henriette Farkas;Gianni Marone;Samuel Luyasu;Bertrand Favier;Ludovic Martin;Kinga Viktória Kőhalmi;György Temesszentandrási;Katalin Várnai;Lilian Varga;Bruce L. Zuraw;Annette Feussner;Michael A. Tortorici;Dipti Pawaskar;Huamin Henry Li;John Anderson;Jonathan A. Bernstein;Ying Zhang;Ingo Pragst;Emel Aygören-Pürsün;Kraig Jacobson;Jim Christensen;Arthur Van Leerberghe;Yi Wang;Jennifer Schranz;Inmaculada Martinez-Saguer;Daniel Soteres;Urs Steiner;Vesna Grivcheva Panovska;William Rae;Werner Aberer;Aarnoud Huissoon;Anette Bygum;Markus Magerl;Jochen Graff;Hilary Longhurst;Ramón Lleonart;Lei Fang;Melanie Cornpropst;Desiree Clemons;Amanda Mathis;Phil Collis;Sylvia Dobo;William P. Sheridan;Marcus Maurer;Marc A. Riedl;Timothy Craig;Aleena Banerji;Mustafa Shennak;William Yang;Jovanna Baptista;Paula Busse;Ira Kalfus;Andrew McDonald;Shawn Qian;Anthony Roberts;Con Panousis;Tim Green;Andreas Gille;Maria Zamanakou;Gedeon Loules;Dorottya Csuka;Fotis Psarros;Faidra Parsopoulou;Matthaios Speletas;Davide Firinu;Tiziana Maria Angela De Pasquale;Alessandra Zoli;Anna Radice;Stefano Pizzimenti;Emmanouil Manoussakis;George N. Konstantinou;Valeria Bafunno;Vincenzo Montinaro;Mauro Cancian;Maurizio Margaglione;Konrad Bork;Karin Wulff;Guenther Witzke;Jochen Hardt;Laurence Bouillet;Teresa Caballero;Anete S. Grumach;Christelle Pommie;Irmgard Andresen;Carmen Escuriola Ettingshausen;Zeynep Gutowski;Karin Andritschke;Richard Linde;Noémi Andrási;Tamás Szilágyi;Iris Leibovich-Nassi;Christine Symons;John Dempster;Isabelle Boccon-Gibod;Anne Pagnier;Audrey Lehmann;Kristian B. Kreiberg;Sandra A. Nieto;Raquel Martins;Renata Martins;Alejandra Menendez;Solange O. R. Valle;Margarita Olivares;Maria E. Hernandez-Landeros;Elma Nievas;Natalia Fili;Olga M. Barrera;René Bailleau;Ana Maria Gallardo-Olivos;Masumi Grau;Julian Rodriguez-Galindo;Marlon J. O. Carabantes;Edison Zapata-Venegas;Mario Martinez Alfonso;Maria Rosario-Grauert;Manuel Ratti;Daniel Vaszquez;Dario Josviack;Luis Fernando Landivar-Salinas;Oscar M. E. Calderón-Llosa;Rolando Campilay-Sarmiento;Pablo Raby;Jose Fabiani;William R. Lumry;Henrike Feuersenger;Douglas J. Watson;Thomas Machnig;Donatella Lamacchia;Adriana Hernanz;Ana Alvez;Mariana Lluncor;Maria Pedrosa;Rosario Cabañas;Nieves Prior;Patrik Nordenfelt;Mats Nilsson;Anders Lindfors;Carl-Fredrik Wahlgren;Janne Björkander;Roman Hakl;Pavel Kuklínek;Irena Krčmová;Jana Hanzlíková;Martina Vachová;Radana Zachová;Marta Sobotková;Jana Strenková;Jiří Litzman;Maria Palasopoulou;Gerasimina Tsinti;Panagiota Gianni;Maria Kompoti;Sofia Garrido;Wojciech Dyga;Anna Bogdali;Aleksander Obtułowicz;Mikolajczyk Tomasz;Ewa Czarnobilska;Krystyna Obtulowicz;Teofila Książek;Anna Koncz;Dominik Gulyás;Maria Staevska;Milos Jesenak;Katarina Hrubiskova;L. Bellizzi;A. Relan;Maddalena A. Wu;Antonio Castelli;Riccardo Colombo;Gianmarco Podda;Marta Del Medico;Emanuele Catena;Francesco Casella;Francesca Perego;Nada Afifi Afifi;Eleonora Tobaldini;Nicola Montano;Marta Sánchez-Jareño;Marcin Stobiecki;Krystyna Obtułowicz;Irina Guryanova;Ekaterina Polyakova;Viktar Lebedz;Andrej Salivonchik;Svetlana Aleshkevich;Mikhail Belevtsev;Melanie Nordmann-Kleiner;Susanne Trainotti;Janina Hahn;Jens Greve;Liudmyla Zabrodska;Maria L. Oliva Alonso;Rosangela P. Tórtora;Alfeu T. França;Marcia G. Ribeiro;Lisa Fu;Amin Kanani;Gina Lacuesta;Susan Waserman;Stephen Betschel;Melissa I. Espinosa;Francisco A. Contreras;Martin Hrubisko;Ludmila Vavrova;Peter Banovcin;Maryam Ayazi;Mohammad Reza Fazlollahi;Shiva Saghafi;Sajedeh Mohammadian;Susan Nabilou Deshiry;Kiana Bidad;Raheleh Shokouhi Shoormasti;Iraj Mohammadzadeh;Mohammad Hassan Bemanian;Seyed Alireza Mahdaviani;Zahra Pourpak;Anna Valerieva;Mariela Vasileva;Tsvetelina Velikova;Elena Petkova;Vasil Dimitrov;Ruggero Di Maulo;Raz Somech;Hava Golander;Erika J. Sifuentes;Catherine Mansard;Anne Gompel;Bernard Floccard;Claire Blanchard-Delaunay;David Launay;Olivier Fain;Alain Sobel;Stéphane Gayet;Stéphanie Amarger;Guillaume Armengol;Yann Ollivier;Ariane Zélinsky-Gurung;Pierre-Yves Jeandel;Gisèle Kanny;Brigitte Coppéré;Marie Dubrel;Fabien Pelletier;Aurélie Du Thanh;Sébastien Trouiller;Jérôme Laurent;Claire De Moreuil;Christine Audouin Pajot;Alexandre Belot;Ana Rodríguez;Dasha Roa;Alicia Prieto;Maria Luisa Baeza;Borislava Krusheva;Stephanie K. A. Almeida;Rosemeire N. Constantino-Silva;Nyla Melo;Joanna Araujo Simoes;Sandra Mitie U. Palma;Jane da Silva;Bruna F. de Azevedo;Eli Mansour;Teresa González-Quevedo;Carmen Marcos;Teófilo Lobera;Blanca Sáenz de San Pedro;Ernie Avilla;Jacquie Badiou;Karen Binkley;Rozita Borici-Mazi;Linda Howlett;Paul K. Keith;Anne Rowe;Peter Waite;Aurore Billebeau;Isabelle Boccon-Gibbod;Kristina Lis;Yael Laitman;Eitan Friedman;N. M. Gokmen;O. Gulbahar;H. Onay;Z. P. Koc;A. Z. Sin
  • 通讯作者:
    A. Z. Sin
52 – Urticaria and Angioedema
52 — 荨麻疹和血管性水肿
Hereditary Angioedema With Normal C1 Inhibitor: A Quarter Century of Forward Progress and Persisting Obstacles
遗传性血管性水肿伴正常 C1 抑制剂:四分之一世纪的进展与持续障碍
  • DOI:
    10.1016/j.jaip.2025.02.036
  • 发表时间:
    2025-06-01
  • 期刊:
  • 影响因子:
    6.600
  • 作者:
    Sandra C. Christiansen;Aleena Banerji;Jonathan A. Bernstein;Paula J. Busse;Timothy Craig;H. Henry Li;Mark Davis-Lorton;William R. Lumry;Marc A. Riedl;Bruce L. Zuraw
  • 通讯作者:
    Bruce L. Zuraw
The US Hereditary Angioedema Association Scientific Registry: hereditary angioedema demographics, disease severity, and comorbidities
  • DOI:
    10.1016/j.anai.2023.08.012
  • 发表时间:
    2023-12-01
  • 期刊:
  • 影响因子:
  • 作者:
    Sandra C. Christiansen;Joyce Wilmot;Anthony J. Castaldo;Bruce L. Zuraw
  • 通讯作者:
    Bruce L. Zuraw

Bruce L. Zuraw的其他文献

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{{ truncateString('Bruce L. Zuraw', 18)}}的其他基金

Mechanisms Underlying the Dominant Negative Phenotype in Hereditary Angioedema
遗传性血管性水肿显性阴性表型的机制
  • 批准号:
    10412915
  • 财政年份:
    2019
  • 资助金额:
    $ 0.23万
  • 项目类别:
Mechanisms Underlying the Dominant Negative Phenotype in Hereditary Angioedema
遗传性血管性水肿显性阴性表型的机制
  • 批准号:
    10516092
  • 财政年份:
    2019
  • 资助金额:
    $ 0.23万
  • 项目类别:
Mechanisms Underlying the Dominant Negative Phenotype in Hereditary Angioedema
遗传性血管性水肿显性阴性表型的机制
  • 批准号:
    10044412
  • 财政年份:
    2019
  • 资助金额:
    $ 0.23万
  • 项目类别:
Dual role of the bradykinin B2 receptor during inflammation
缓激肽 B2 受体在炎症过程中的双重作用
  • 批准号:
    7929357
  • 财政年份:
    2010
  • 资助金额:
    $ 0.23万
  • 项目类别:
Dual role of the bradykinin B2 receptor during inflammation
缓激肽 B2 受体在炎症过程中的双重作用
  • 批准号:
    8196318
  • 财政年份:
    2010
  • 资助金额:
    $ 0.23万
  • 项目类别:
Dual role of the bradykinin B2 receptor during inflammation
缓激肽 B2 受体在炎症过程中的双重作用
  • 批准号:
    8391112
  • 财政年份:
    2010
  • 资助金额:
    $ 0.23万
  • 项目类别:
CLINICAL TRIAL: PHASE II STUDY OF THE SAFETY & EFFICACY OF RECOMBINANT HUMAN C1
临床试验:第二阶段安全性研究
  • 批准号:
    8166834
  • 财政年份:
    2009
  • 资助金额:
    $ 0.23万
  • 项目类别:
CLINICAL TRIAL: PHASE II STUDY OF THE SAFETY & EFFICACY OF RECOMBINANT HUMAN C1
临床试验:第二阶段安全性研究
  • 批准号:
    7950979
  • 财政年份:
    2008
  • 资助金额:
    $ 0.23万
  • 项目类别:
CLINICAL TRIAL: PHARMACOKINETICS OF C1INH-NF IN HEREDITARY ANGIOEDEMA SUBJECTS
临床试验:C1INH-NF 在遗传性血管水肿受试者中的药代动力学
  • 批准号:
    7724962
  • 财政年份:
    2007
  • 资助金额:
    $ 0.23万
  • 项目类别:
CLINICAL TRIAL: PHASE II STUDY OF THE SAFETY & EFFICACY OF RECOMBINANT HUMAN C1
临床试验:第二阶段安全性研究
  • 批准号:
    7724969
  • 财政年份:
    2007
  • 资助金额:
    $ 0.23万
  • 项目类别:

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Study on molecular basis of expression and structure of complement component C1s/C1r/C1r-LP
补体成分C1s/C1r/C1r-LP表达及结构的分子基础研究
  • 批准号:
    18590634
  • 财政年份:
    2006
  • 资助金额:
    $ 0.23万
  • 项目类别:
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