EFFECTS OF MULTIPLE DOSE ENZYME REPLACEMENT USING CEREDASE IN GAUCHER'S DISEASE

使用 CEREDASE 进行多剂量酶替代治疗戈谢病的效果

• 批准号: 6279984
• 负责人: HENRY J MANKIN
• 金额: $ 2.74万
• 依托单位: MASSACHUSETTS GENERAL HOSPITAL
• 依托单位国家: 美国
• 财政年份: 1997
• 资助国家: 美国
• 起止时间: 1997-12-01 至 1998-11-30
• 项目状态: 已结题
• 来源: https://reporter.nih.gov/project-details/6279984
• 关键词: Gaucher's disease; bone disorder; clinical research; clinical trial phase I; dosage; enzyme therapy; glucosylceramidase; human subject; human therapy evaluation; macrophage; metabolism disorder chemotherapy; patient care management

The first stage of this study will continue the analysis of the results of management of a cohort of patients with Type I Gauchers disease under treatment with macrophage targeted glucocerebrosidase with particular attention to bone disease.

本研究的第一阶段将继续对结果进行分析 治疗一组I型戈谢病患者， 用巨噬细胞靶向的葡糖脑苷脂酶治疗， 注意骨骼疾病。