TRIAL OF VALPROIC ACID AND CARNITINE IN PATIENTS WITH SPINAL MUSCULAR ATROPHY

丙戊酸和肉碱在脊髓性肌萎缩症患者中的试验

• 批准号: 7625461
• 负责人: JOHN C KISSEL
• 金额: $ 21.94万
• 依托单位: OHIO STATE UNIVERSITY
• 依托单位国家: 美国
• 财政年份: 2007
• 资助国家: 美国
• 起止时间: 2007-04-23 至 2007-11-30
• 项目状态: 已结题
• 来源: https://reporter.nih.gov/project-details/7625461
• 关键词: Age-Years; Carnitine; Computer Retrieval of Information on Scientific Projects Database; Funding; Grant; Institution; Oral; Patients; Research; Research Personnel; Resources; Safety; Source; Spinal Muscular Atrophy; Treatment Protocols; United States National Institutes of Health; Valproic Acid

This subproject is one of many research subprojects utilizing the resources provided by a Center grant funded by NIH/NCRR. The subproject and investigator (PI) may have received primary funding from another NIH source, and thus could be represented in other CRISP entries. The institution listed is for the Center, which is not necessarily the institution for the investigator. The primary objective is to assess the safety, tolerability, and efficacy of a combined regimen of oral valproic acid (VPA) and carnitine in SMA patients 2-17 years of age.

这个子项目是许多研究子项目中的一个 由NIH/NCRR资助的中心赠款提供的资源。子项目和 研究者（PI）可能从另一个NIH来源获得了主要资金， 因此可以在其他CRISP条目中表示。所列机构为 研究中心，而研究中心不一定是研究者所在的机构。 主要目的是评估口服丙戊酸（VPA）和肉毒碱联合治疗方案在2-17岁SMA患者中的安全性、耐受性和疗效。