GAUCHER REGISTRY

本子项目是利用由NIH/NCRR资助的中心赠款提供的资源的众多研究子项目之一。子项目和研究者（PI）可能已经从另一个NIH来源获得了主要资金，因此可以在其他CRISP条目中表示。列出的机构是中心的，不一定是研究者的机构。戈谢病注册是一个正在进行的、上市后的观察性数据库，用于跟踪戈谢病患者常规临床实践的结果。并不是所有登记的患者都在接受酶替代疗法（ERT）。所有参与注册的医生都被认为是国际合作戈歇小组（ICGG）的成员。从ICGG医生收集的数据将代表常见临床条件下戈谢病的实践模式。因此，这个国际协作登记所收集的数据将提供信息，以更好地描述戈谢病的自然史和进展，以及医生开ERT的患者的临床反应。

This subproject is one of many research subprojects utilizing the resources provided by a Center grant funded by NIH/NCRR. The subproject and investigator (PI) may have received primary funding from another NIH source, and thus could be represented in other CRISP entries. The institution listed is for the Center, which is not necessarily the institution for the investigator. The Gaucher Registry is an ongoing, post-marketing, observational database that tracks outcomes of routine clinical practice for patients with Gaucher disease. Not all patients in the Registry are on Enzyme Replacement Therapy (ERT). All physicians participating in the Registry are considered members of the International Collaborative Gaucher Group (ICGG). Data collected from ICGG physicians will represent Gaucher disease practice patterns under common clinical conditions. Thus, the data collected by this international, collaborative Registry will provide information to better characterize the natural history and progression of Gaucher disease, as well as the clinical responses of patients whose physicians have prescribed ERT.