GAUCHER REGISTRY

这个子项目是许多研究子项目中利用 资源由NIH/NCRR资助的中心拨款提供。子项目和 调查员(PI)可能从NIH的另一个来源获得了主要资金， 并因此可以在其他清晰的条目中表示。列出的机构是 该中心不一定是调查人员的机构。 高谢病登记处是一个持续的、上市后的观察性数据库，跟踪高谢病患者常规临床实践的结果。并不是登记的所有患者都在接受酶替代疗法(ERT)。所有参加注册的医生都被认为是国际合作高谢尔小组(ICGG)的成员。从ICGG医生那里收集的数据将代表常见临床条件下的高谢病实践模式。因此，这一国际合作登记收集的数据将提供信息，以更好地描述高谢病的自然病史和进展，以及医生开出ERT处方的患者的临床反应。

This subproject is one of many research subprojects utilizing the resources provided by a Center grant funded by NIH/NCRR. The subproject and investigator (PI) may have received primary funding from another NIH source, and thus could be represented in other CRISP entries. The institution listed is for the Center, which is not necessarily the institution for the investigator. The Gaucher Registry is an ongoing, post-marketing, observational database that tracks outcomes of routine clinical practice for patients with Gaucher disease. Not all patients in the Registry are on Enzyme Replacement Therapy (ERT). All physicians participating in the Registry are considered members of the International Collaborative Gaucher Group (ICGG). Data collected from ICGG physicians will represent Gaucher disease practice patterns under common clinical conditions. Thus, the data collected by this international, collaborative Registry will provide information to better characterize the natural history and progression of Gaucher disease, as well as the clinical responses of patients whose physicians have prescribed ERT.