Novel Molecular Mechanisms of Neuromuscular Disease: Implications for Therapy

描述(申请人提供)：本申请提出一个国际会议，题为：“神经肌肉疾病的新分子机制：对治疗的影响”。这次会议将把来自学术界、基金会和制药行业的翻译和临床科学家聚集在一个合议性论坛上。这项提议是由联合主席与肌肉研究小组的领导共同制定的。这次会议向肌肉研究小组、英国神学学会和其他团体开放，也欢迎目前没有隶属于研究小组的个人参加。优先考虑提交研究报告的调查人员 以供演示。这次会议的科学重点将放在许多关键的“交叉”主题上，这些主题是多种神经肌肉疾病的共同之处，具有重要的临床和翻译潜力。会议将在一个环境中举行，将把高级调查人员、制药公司的代表、国家卫生研究院项目工作人员、基金会和患者倡导代表以及初级/见习调查人员聚集在一起。会议为学员和初级教员提供了开发神经肌肉疾病新疗法的策略的视角。会议的环境和形式非常适合现有调查员之间以及高级调查员和新任/初级调查员之间的协作互动/发展。预计会议将继续在与会者之间带来新的合作。所有与会者将被邀请提交他们的作品，并参加互动海报讨论会议。将鼓励和支持受训人员参加并介绍他们自己的工作。这次会议旨在鼓励住院医生、实习生和初级教员在实验治疗学方面追求职业生涯。

DESCRIPTION (provided by applicant): This application proposes an international conference entitled: "Novel Molecular Mechanisms of Neuromuscular Disease: Implications for Therapy". The conference will bring together translational and clinical scientists from academia, foundations, and pharma in a collegial forum. This proposal has been developed by co-chairs working with the leadership of the Muscle Study Group. The conference is open to attendance from the Muscle Study Group, The British Myology Society and other groups and by individuals not currently affiliated with a study group. Priority is given to investigators submitting research for presentation. The conference's scientific emphasis will be on a number of key "cross cutting" themes that are common to multiple neuromuscular disorders and have important clinical and translational potential. The conference will be held in an environment that will bring senior investigators, representatives of pharma, National Institutes of Health program staff, and foundation and patient advocacy representatives together with junior/trainee investigators. The conference provides perspective for trainees and junior faculty in the strategies for developing novel treatments for neuromuscular diseases. The setting and the meeting format are ideal for interaction/development of collaboration among established investigators and between senior and new/junior investigators. It is expected that the conference will continue to lead to new collaboration among attendees. All attendees will be invited to submit their work and to participate in interactive poster discussion sessions. Trainees will be encouraged and supported to attend and to present their own work. The conference is designed to encourage residents, trainees and junior faculty to pursuing a career in experimental therapeutics.