Novel Molecular Mechanisms of Neuromuscular Disease: Implications for Therapy

神经肌肉疾病的新分子机制：对治疗的影响

基本信息

批准号：
8597196
负责人：
Robert C Griggs
金额：
$ 3.6万
依托单位：
UNIVERSITY OF ROCHESTER
依托单位国家：
美国
项目类别：
财政年份：
2013
资助国家：
美国
起止时间：
2013-08-01 至 2014-07-31
项目状态：
已结题

来源：
https://reporter.nih.gov/project-details/8597196
关键词：
Academia Animal Model Attention British Buffaloes Clinical Clinical Investigator Clinical Research Clinical Trials Collaborations Development Disease Educational workshop Environment European Faculty Fostering Foundations Funding Future Genetic Transcription Goals Individual Industry International International Aspects Lead Leadership Learning London Mentors Methods Molecular Muscle Myopathy Neuromuscular Diseases Pathogenesis Patient advocacy Patients Proteins RNA Splicing Research Research Personnel Research Proposals Scientist Site Societies Therapeutic Time United States National Institutes of Health Universities Work base bench to bedside career college cost design expectation experience improved meetings novel novel strategies posters programs public health relevance skills symposium translational clinical trial translational neuroscience

项目摘要

DESCRIPTION (provided by applicant): This application proposes an international conference entitled: "Novel Molecular Mechanisms of Neuromuscular Disease: Implications for Therapy". The conference will bring together translational and clinical scientists from academia, foundations, and pharma in a collegial forum. This proposal has been developed by co-chairs working with the leadership of the Muscle Study Group. The conference is open to attendance from the Muscle Study Group, The British Myology Society and other groups and by individuals not currently affiliated with a study group. Priority is given to investigators submitting research for presentation. The conference's scientific emphasis will be on a number of key "cross cutting" themes that are common to multiple neuromuscular disorders and have important clinical and translational potential. The conference will be held in an environment that will bring senior investigators, representatives of pharma, National Institutes of Health program staff, and foundation and patient advocacy representatives together with junior/trainee investigators. The conference provides perspective for trainees and junior faculty in the strategies for developing novel treatments for neuromuscular diseases. The setting and the meeting format are ideal for interaction/development of collaboration among established investigators and between senior and new/junior investigators. It is expected that the conference will continue to lead to new collaboration among attendees. All attendees will be invited to submit their work and to participate in interactive poster discussion sessions. Trainees will be encouraged and supported to attend and to present their own work. The conference is designed to encourage residents, trainees and junior faculty to pursuing a career in experimental therapeutics.

描述（由申请人提供）：本申请提出了一个国际会议，标题为“神经肌肉疾病的新分子机制：对治疗的影响”。该会议将在一个大学论坛上汇集来自学术界，基金会和制药的转化和临床科学家。该提案是由与肌肉研究小组领导的联合主席制定的。该会议开放肌肉研究小组，英国肉体学协会和其他小组以及目前尚未与研究小组相关的个人。优先授予调查人员提交研究用于演示。会议的科学重点将是许多关键的“交叉切割”主题，这些主题是多种神经肌肉疾病常见的，并且具有重要的临床和转化潜力。该会议将在一个环境中举行，该环境将与初级/受训者的调查员一起，将高级调查员，制药公司的代表，国立卫生研究院工作人员以及基金会和患者倡导代表以及患者倡导代表一起举行。该会议为受训者和初级教师提供了开发神经肌肉疾病新颖治疗的策略的观点。设置和会议格式非常适合既定研究人员之间以及新高级和初级调查人员之间协作的互动/开发。预计会议将继续导致与会者之间的新合作。所有与会者将被邀请提交工作并参加互动海报讨论会议。受训人员将受到鼓励和支持，参加并介绍自己的工作。该会议旨在鼓励居民，学员和初级教职员工从事实验性治疗事业。