Novel Molecular Mechanisms of Neuromuscular Disease: Implications for Therapy

描述（由申请人提供）： 本申请提出了一个国际会议，题为：“神经肌肉疾病的新分子机制：对治疗的启示”。会议将汇集来自学术界、基金会和制药公司的翻译和临床科学家参加一个合议论坛。该提案由联合主席与肌肉研究小组的领导合作制定。会议对肌肉研究小组、英国肌肉学会和其他团体以及目前不属于研究小组的个人开放。优先考虑提交研究的研究者 用于展示。会议的科学重点将是一些关键的“交叉”主题，这些主题是多种神经肌肉疾病的共同点，具有重要的临床和转化潜力。会议将在一个环境中举行，该环境将使高级研究人员，制药公司代表，美国国立卫生研究院项目工作人员，基金会和患者倡导代表与初级/实习研究人员一起。会议为学员和初级教师提供了开发神经肌肉疾病新疗法的策略。会议的环境和形式非常适合现有研究者之间以及高级和新/初级研究者之间的互动/发展合作。预计会议将继续导致与会者之间的新合作。所有与会者将被邀请提交他们的工作，并参加互动海报讨论会。将鼓励和支持受训人员参加会议并介绍自己的工作。该会议旨在鼓励居民，学员和初级教师追求实验治疗学的职业生涯。

DESCRIPTION (provided by applicant): This application proposes an international conference entitled: "Novel Molecular Mechanisms of Neuromuscular Disease: Implications for Therapy". The conference will bring together translational and clinical scientists from academia, foundations, and pharma in a collegial forum. This proposal has been developed by co-chairs working with the leadership of the Muscle Study Group. The conference is open to attendance from the Muscle Study Group, The British Myology Society and other groups and by individuals not currently affiliated with a study group. Priority is given to investigators submitting research for presentation. The conference's scientific emphasis will be on a number of key "cross cutting" themes that are common to multiple neuromuscular disorders and have important clinical and translational potential. The conference will be held in an environment that will bring senior investigators, representatives of pharma, National Institutes of Health program staff, and foundation and patient advocacy representatives together with junior/trainee investigators. The conference provides perspective for trainees and junior faculty in the strategies for developing novel treatments for neuromuscular diseases. The setting and the meeting format are ideal for interaction/development of collaboration among established investigators and between senior and new/junior investigators. It is expected that the conference will continue to lead to new collaboration among attendees. All attendees will be invited to submit their work and to participate in interactive poster discussion sessions. Trainees will be encouraged and supported to attend and to present their own work. The conference is designed to encourage residents, trainees and junior faculty to pursuing a career in experimental therapeutics.