9th International Myotonic Dystrophy Consortium Meeting

项目摘要/摘要(说明) 本申请申请为国际强直性肌营养不良协会第9届会议申请资金 (IDMC-9)。IDMC-9定于2013年10月16日至10月19日在西班牙圣塞巴斯蒂安召开。 这次会议将汇集来自世界各地的顶尖科学家，讨论高影响力， 强直性肌营养不良(DM)的跨学科研究。这次会议的目的是促进科学研究 讨论和促进跨学科交流。这次会议汇聚了全球领先的基础研究人员 该领域的临床医生和临床研究人员代表广泛的专业领域，包括： 神经学、心脏病学、麻醉学、临床试验、神经生物学、病理学、遗传学和分子生物学。 他们的互动和讨论激发了研究和临床护理的新方法，并提供了 发展和加强合作学习的机会。IDMC-9的一个新焦点包括计划 培养该领域的下一代领导者，并让他们参与到“临床试验”的讨论中来 鉴于有希望的实验和治疗突破，这样的讨论是必要的 在糖尿病动物模型中。 IDMC-9的第一天将包括：登记；关于评估疾病的成果衡量的卫星专题讨论会 强直性肌营养不良的进展；主旨演讲；以及欢迎招待会。接下来的三天 会议将专门用于科学会议，在这些会议上，研究人员和临床医生将进行同行审查， 基础、临床和翻译研究主题的精选摘要。科学会议上午8：00开始。 每天下午5：30到7：30结束。将有两个正式的海报会议。海报将会是 在整个会议期间显示。在IDMC-9上的所有会议都将集中于“前沿”主题和 糖尿病的发病机制、动物和细胞模型、临床及治疗等方面的研究。 疾病症状和治疗进展。 在最后一天，将有以患者为导向的会议，以促进患者、护理人员、 患者权益倡导团体、临床医生和调查人员的代表。这些会议将以“非专业”的方式进行 鼓励患者和研究人员之间的互动和思想交流。这场决赛的下午 这一天将以前几届会议的亮点开始，随后是倡导小组的演讲，以及 会议接受患者和家属的提问和回答。

Project Summary/Abstract (Description) This application requests funding for the 9th meeting of the International Myotonic Dystrophy Consortium (IDMC-9). IDMC-9 is scheduled to convene in San Sebasti¿n, Spain from October 16th to October 19th, 2013. The conference will bring together top scientists from around the world to discuss high-impact, interdisciplinary research on myotonic dystrophy (DM). The objective of the conference is to promote scientific discussion and facilitate interdisciplinary exchange. This meeting brings together leading basic researchers in the field with clinicians and clinical investigators representing a broad range of specialties including: neurology, cardiology, anesthesiology, clinical trials, neurobiology, pathology, genetics and molecular biology. Their interactions and discussions stimulate new approaches to research and clinical care and provide opportunities to develop and strengthen collaborative studies. One new focus at IDMC-9 includes plans to nurture the next-generation leaders of the field and involve them in discussions on "clinical trial preparedness." Such discussions are needed in light of promising experimental and therapeutic breakthroughs in animal models of DM. The first day of IDMC-9 will include: registration; a satellite symposium on outcome measures to assess disease progression in myotonic dystrophy; keynote lectures; and a welcoming reception. The subsequent three days of the meeting will be devoted to scientific sessions in which researchers and clinicians present peer-reviewed, selected abstracts on basic, clinical and translational research topics. The scientific sessions begin at 8:00 AM and conclude between 5:30 to 7:30 PM each day. There will be two formal poster sessions. Posters will be displayed during the entire meeting. All the sessions at IDMC-9 will focus on "cutting edge" topics and research, such as, disease mechanisms of DM, animal and cell models, clinical aspects and management of disease symptoms, and therapeutic development. On the final day, there will be patient-oriented sessions to promote discussion among patients, care-givers, representatives of patient advocacy groups, clinicians, and investigators. These sessions will be in "lay" terms to encourage interaction and exchanges of ideas among patients and investigators. The afternoon of this final day will begin with highlights from the previous sessions, followed by advocacy group presentations, and a session for questions and answers from patients and family members.