9th International Myotonic Dystrophy Consortium Meeting

第九届国际强直性肌营养不良联盟会议

• 批准号: 8651262
• 负责人: RICHARD T MOXLEY
• 金额: $ 2万
• 依托单位: UNIVERSITY OF ROCHESTER
• 依托单位国家: 美国
• 财政年份: 2013
• 资助国家: 美国
• 起止时间: 2013-09-30 至 2014-08-31
• 项目状态: 已结题
• 来源: https://reporter.nih.gov/project-details/8651262
• 关键词: Adult; Advocacy; Advocate; Affect; Age; Anesthesiology; Animal Model; Basic Science; Brain; Cardiology; Caregivers; Caring; Cell model; Clinical; Clinical Investigator; Clinical Research; Clinical Trials; Collaborations; Data; Defect; Development; Development Plans; Devices; Disease; Disease Management; Disease Progression; Endocrine system; Environment; Eye; Family Caregiver; Family Planning; Family member; Foundations; Functional disorder; Funding; Funding Agency; Future; Gene Expression Profile; Genetic; Goals; Grant; Growth; Heart; Human; Industry; Interdisciplinary Study; International; Investigational Therapies; Lead; Light; Medical Economics; Medicine; Mind; Modality; Molecular Biology; Muscle Fibers; Muscular Dystrophies; Myotonia; Myotonic Dystrophy; Neurobiology; Neurology; Neurons; Outcome Measure; Pathology; Patient Care; Patients; Peer Review; Pharmaceutical Preparations; Provider; Quality of life; RNA; Readiness; Request for Applications; Research; Research Infrastructure; Research Personnel; Schedule; Scientist; Senior Scientist; Skeletal Muscle; Spain; Structure; Symptoms; System; Therapeutic; Time; Toxic effect; Translational Research; Work; abstracting; bench to bedside; career; clinical care; efficacy testing; gastrointestinal system; induced pluripotent stem cell; innovation; lectures; medical specialties; meetings; molecular pathology; mouse model; multidisciplinary; next generation; novel strategies; optimism; patient advocacy group; patient oriented; posters; public health relevance; success; symposium; therapeutic development

Project Summary/Abstract (Description) This application requests funding for the 9th meeting of the International Myotonic Dystrophy Consortium (IDMC-9). IDMC-9 is scheduled to convene in San Sebasti¿n, Spain from October 16th to October 19th, 2013. The conference will bring together top scientists from around the world to discuss high-impact, interdisciplinary research on myotonic dystrophy (DM). The objective of the conference is to promote scientific discussion and facilitate interdisciplinary exchange. This meeting brings together leading basic researchers in the field with clinicians and clinical investigators representing a broad range of specialties including: neurology, cardiology, anesthesiology, clinical trials, neurobiology, pathology, genetics and molecular biology. Their interactions and discussions stimulate new approaches to research and clinical care and provide opportunities to develop and strengthen collaborative studies. One new focus at IDMC-9 includes plans to nurture the next-generation leaders of the field and involve them in discussions on "clinical trial preparedness." Such discussions are needed in light of promising experimental and therapeutic breakthroughs in animal models of DM. The first day of IDMC-9 will include: registration; a satellite symposium on outcome measures to assess disease progression in myotonic dystrophy; keynote lectures; and a welcoming reception. The subsequent three days of the meeting will be devoted to scientific sessions in which researchers and clinicians present peer-reviewed, selected abstracts on basic, clinical and translational research topics. The scientific sessions begin at 8:00 AM and conclude between 5:30 to 7:30 PM each day. There will be two formal poster sessions. Posters will be displayed during the entire meeting. All the sessions at IDMC-9 will focus on "cutting edge" topics and research, such as, disease mechanisms of DM, animal and cell models, clinical aspects and management of disease symptoms, and therapeutic development. On the final day, there will be patient-oriented sessions to promote discussion among patients, care-givers, representatives of patient advocacy groups, clinicians, and investigators. These sessions will be in "lay" terms to encourage interaction and exchanges of ideas among patients and investigators. The afternoon of this final day will begin with highlights from the previous sessions, followed by advocacy group presentations, and a session for questions and answers from patients and family members.

项目概要/摘要（描述） 本申请要求为国际强直性肌营养不良症联盟第9次会议提供资金 （IDMC-9）。IDMC-9定于2013年10月16日至10月19日在西班牙圣塞瓦斯蒂恩召开。 会议将汇集来自世界各地的顶尖科学家，讨论高影响力， 强直性肌营养不良（DM）的跨学科研究。会议的目的是促进科学 促进跨学科交流。本次会议汇集了领先的基础研究人员， 该领域的临床医生和临床研究人员代表广泛的专业，包括： 神经病学、心脏病学、麻醉学、临床试验、神经生物学、病理学、遗传学和分子生物学。 他们的互动和讨论激发了研究和临床护理的新方法， 发展和加强合作研究的机会。IDMC-9的一个新重点包括计划 培养该领域的下一代领导者，并让他们参与“临床试验”的讨论 做好准备“鉴于有希望的实验和治疗突破， 在糖尿病动物模型中。 IDMC-9的第一天将包括：登记;关于评估疾病结果措施的卫星研讨会 强直性肌营养不良的进展;主题演讲;和欢迎招待会。随后的三天 会议的一部分将专门用于科学会议，其中研究人员和临床医生提出同行评审， 基础、临床和转化研究主题的精选摘要。科学会议开始在上午8：00 每天下午5：30到7：30结束。将有两个正式的海报会议。海报将 在整个会议期间展示。IDMC-9的所有会议都将重点关注“前沿”主题， 研究，如糖尿病的疾病机制，动物和细胞模型，临床方面和管理， 疾病症状和治疗进展。 在最后一天，将有以病人为导向的会议，以促进病人，护理人员， 患者权益团体、临床医生和研究者的代表。这些会议将在“奠定”条款 鼓励患者和研究者之间的互动和交流。决赛当天下午 开始时将介绍前几次会议的重点，然后是宣传小组的介绍， 为病人和家属的提问和解答。