TKT024EXT: MPS II PATIENTS RECEIVING IDURONATE-2-SULFATASE ENZYME REPLACEMENT

TKT024EXT：接受艾杜糖酸-2-硫酸酯酶替代的 MPS II 患者

• 批准号: 7377529
• 负责人: JOSEPH J. MUENZER
• 金额: $ 8.08万
• 依托单位: UNIV OF NORTH CAROLINA CHAPEL HILL
• 依托单位国家: 美国
• 财政年份: 2005
• 资助国家: 美国
• 起止时间: 2005-12-01 至 2006-11-30
• 项目状态: 已结题
• 来源: https://reporter.nih.gov/project-details/7377529
• 关键词: TKT024EXT; MPS; II; PATIENTS; RECEIVING

This subproject is one of many research subprojects utilizing the resources provided by a Center grant funded by NIH/NCRR. The subproject and investigator (PI) may have received primary funding from another NIH source, and thus could be represented in other CRISP entries. The institution listed is for the Center, which is not necessarily the institution for the investigator. The primary objective of this extension study is to collect long-term safety and clinical outcome data in MPS II patients receiving enzyme replacement therapy with idursulfase.

该子项目是利用NIH/NCRR资助的中心赠款提供的资源的许多研究子项目之一。子项目和研究者（PI）可能从另一个NIH来源获得主要资金，因此可以在其他CRISP条目中表示。所列机构为中心，不一定是研究者所在机构。本扩展研究的主要目的是收集接受艾度硫酸酯酶酶替代治疗的MPS II患者的长期安全性和临床结局数据。