TKT024EXT: MPS II PATIENTS RECEIVING IDURONATE-2-SULFATASE ENZYME REPLACEMENT

TKT024EXT：接受艾杜糖酸-2-硫酸酯酶替代的 MPS II 患者

• 批准号: 7625579
• 负责人: JOSEPH J. MUENZER
• 金额: $ 2.25万
• 依托单位: UNIV OF NORTH CAROLINA CHAPEL HILL
• 依托单位国家: 美国
• 财政年份: 2006
• 资助国家: 美国
• 起止时间: 2006-12-01 至 2007-11-30
• 项目状态: 已结题
• 来源: https://reporter.nih.gov/project-details/7625579
• 关键词: Clinical; Computer Retrieval of Information on Scientific Projects Database; Data; Enzymes; Funding; Grant; Idursulfase; Institution; Mucopolysaccharidosis II; Outcome; Patients; Research; Research Personnel; Resources; Safety; Source; United States National Institutes of Health; enzyme replacement therapy; iduronate-2-sulfatase

This subproject is one of many research subprojects utilizing the resources provided by a Center grant funded by NIH/NCRR. The subproject and investigator (PI) may have received primary funding from another NIH source, and thus could be represented in other CRISP entries. The institution listed is for the Center, which is not necessarily the institution for the investigator. The primary objective of this extension study is to collect long-term safety and clinical outcome data in MPS II patients receiving enzyme replacement therapy with idursulfase.

这个子项目是许多研究子项目中利用 资源由NIH/NCRR资助的中心拨款提供。子项目和 调查员(PI)可能从NIH的另一个来源获得了主要资金， 并因此可以在其他清晰的条目中表示。列出的机构是 该中心不一定是调查人员的机构。 这项扩展研究的主要目的是收集接受艾杜硫酶酶替代治疗的MPS II患者的长期安全性和临床结果数据。