TKT024EXT: MPS II PATIENTS RECEIVING IDURONATE-2-SULFATASE ENZYME REPLACEMENT
TKT024EXT: MPS II PATIENTS RECEIVING IDURONATE-2-SULFATASE ENZYME REPLACEMENT
批准号:
7716800
负责人:
JOSEPH J. MUENZER
金额:
$0.13万
依托单位国家:
美国
项目类别:
财政年份:
2008
资助国家:
美国
项目状态:
已结题
起止时间:
2008-04-02 至 2008-05-31
中文摘要
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英文摘要
This subproject is one of many research subprojects utilizing the
resources provided by a Center grant funded by NIH/NCRR. The subproject and
investigator (PI) may have received primary funding from another NIH source,
and thus could be represented in other CRISP entries. The institution listed is
for the Center, which is not necessarily the institution for the investigator.
The primary objective of this extension study is to collect long-term safety and clinical outcome data in MPS II patients receiving enzyme replacement therapy with idursulfase.
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CLINICAL TRIAL: MAINTENANCE STUDY OF IDURONATE-2-SULFATASE REPLACEMENT THERAPY I
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批准号:7716755
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项目类别:
-
资助金额:$0.02万
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财政年份:2008
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负责人:JOSEPH J. MUENZER
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依托单位:
MAINTENANCE STUDY OF IDURONATE-2-SULFATASE REPLACEMENT THERAPY IN MPS II PATIENT
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批准号:7625515
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项目类别:
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资助金额:$0.53万
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财政年份:2006
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负责人:JOSEPH J. MUENZER
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依托单位:
TKT024EXT: MPS II PATIENTS RECEIVING IDURONATE-2-SULFATASE ENZYME REPLACEMENT
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批准号:7625579
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项目类别:
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资助金额:$2.25万
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财政年份:2006
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负责人:JOSEPH J. MUENZER
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依托单位:
MAINTENANCE STUDY OF IDURONATE-2-SULFATASE REPLACEMENT THERAPY IN MPS II PATIENT
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批准号:7377421
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项目类别:
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资助金额:$0.89万
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财政年份:2005
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负责人:JOSEPH J. MUENZER
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依托单位:
TKT024EXT: MPS II PATIENTS RECEIVING IDURONATE-2-SULFATASE ENZYME REPLACEMENT
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批准号:7377529
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项目类别:
-
资助金额:$8.08万
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财政年份:2005
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负责人:JOSEPH J. MUENZER
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依托单位:
BI-WEEKLY DOSING REGIMENS OF IDURONATE-2-SULFATASE ENZYME REPLACEMENT MPS II
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批准号:7377468
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项目类别:
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资助金额:$1.39万
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财政年份:2005
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负责人:JOSEPH J. MUENZER
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依托单位:
MAINTENANCE STUDY OF IDURONATE-2-SULFATASE REPLACEMENT THERAPY IN MPS II PATIENT
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批准号:7200214
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项目类别:
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资助金额:$2.76万
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财政年份:2004
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负责人:JOSEPH J. MUENZER
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依托单位:
TKT024EXT: MPS II PATIENTS RECEIVING IDURONATE-2-SULFATASE ENZYME REPLACEMENT
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批准号:7200330
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项目类别:
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资助金额:$0.28万
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财政年份:2004
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负责人:JOSEPH J. MUENZER
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依托单位:
BI-WEEKLY DOSING REGIMENS OF IDURONATE-2-SULFATASE ENZYME REPLACEMENT MPS II
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批准号:7200278
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项目类别:
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资助金额:$18.54万
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财政年份:2004
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负责人:JOSEPH J. MUENZER
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依托单位:
MPS II: Validation of Childhood Health Assessment Questionnaire
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批准号:6980721
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项目类别:
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资助金额:$0.11万
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财政年份:2003
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负责人:JOSEPH J. MUENZER
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依托单位:
Maintenance Study of Iduronate-2-Sulfatase Replacement Therapy in MPS II Patient
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批准号:6980643
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项目类别:
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资助金额:$8.26万
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财政年份:2003
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负责人:JOSEPH J. MUENZER
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依托单位:
Bi-Weekly Dosing Regimens of Iduronate-2-Sulfatase Enzyme Replacement MPS II
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批准号:6980716
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项目类别:
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资助金额:$2.18万
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财政年份:2003
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负责人:JOSEPH J. MUENZER
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依托单位:
ENZYME REPLACEMENT THERAPY FOR PATIENT W/ MUCOPOLYSACCHARIDOSIS I
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批准号:6566103
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项目类别:
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资助金额:$19.07万
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财政年份:2001
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负责人:JOSEPH J. MUENZER
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依托单位:
ENZYME REPLACEMENT THERAPY FOR PATIENT W/ MUCOPOLYSACCHARIDOSIS I
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批准号:6504251
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项目类别:
-
资助金额:$19.07万
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财政年份:2000
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负责人:JOSEPH J. MUENZER
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依托单位:
ENZYME REPLACEMENT THERAPY FOR PATIENT W/ MUCOPOLYSACCHARIDOSIS I
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批准号:6423274
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项目类别:
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资助金额:$29.46万
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财政年份:2000
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负责人:JOSEPH J. MUENZER
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依托单位:
ENZYME REPLACEMENT THERAPY FOR PATIENT W/ MUCOPOLYSACCHARIDOSIS I
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批准号:6303934
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项目类别:
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资助金额:$0.02万
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财政年份:1999
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负责人:JOSEPH J. MUENZER
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依托单位:
ENZYME REPLACEMENT THERAPY FOR PATIENT W/ MUCOPOLYSACCHARIDOSIS I
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批准号:6263894
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项目类别:
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资助金额:$0.02万
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财政年份:1998
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负责人:JOSEPH J. MUENZER
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依托单位:
ENZYME REPLACEMENT THERAPY FOR PATIENT W/ MUCOPOLYSACCHARIDOSIS I
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批准号:6297262
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项目类别:
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资助金额:$0.02万
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财政年份:1998
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负责人:JOSEPH J. MUENZER
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依托单位:
MOLECULAR GENETICS OF IDURONATE SULFATASE DEFICIENCIES
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批准号:3462552
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项目类别:
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资助金额:$10.51万
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财政年份:1987
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负责人:JOSEPH J. MUENZER
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依托单位:
MOLECULAR GENETICS OF IDURONATE SULFATASE DEFICIENCIES
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批准号:3462553
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项目类别:
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资助金额:$10.73万
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财政年份:1987
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负责人:JOSEPH J. MUENZER
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依托单位: