MAINTENANCE STUDY OF IDURONATE-2-SULFATASE REPLACEMENT THERAPY IN MPS II PATIENT

MPS II 患者艾杜糖酸-2-硫酸酯酶替代治疗的维持研究

• 批准号: 7625515
• 负责人: JOSEPH J. MUENZER
• 金额: $ 0.53万
• 依托单位: UNIV OF NORTH CAROLINA CHAPEL HILL
• 依托单位国家: 美国
• 财政年份: 2006
• 资助国家: 美国
• 起止时间: 2006-12-01 至 2007-11-30
• 项目状态: 已结题
• 来源: https://reporter.nih.gov/project-details/7625515
• 关键词: Computer Retrieval of Information on Scientific Projects Database; Effectiveness; Enzymes; Funding; Grant; Institution; Maintenance; Mucopolysaccharidosis II; Patients; Purpose; Replacement Therapy; Research; Research Personnel; Resources; Safety; Source; Testing; United States National Institutes of Health; iduronate-2-sulfatase; research study

This subproject is one of many research subprojects utilizing the resources provided by a Center grant funded by NIH/NCRR. The subproject and investigator (PI) may have received primary funding from another NIH source, and thus could be represented in other CRISP entries. The institution listed is for the Center, which is not necessarily the institution for the investigator. The purpose of this research study is to continue to test the safety and effectiveness of the experimental enzyme, iduronate-2-sulfatase (I2S) replacement treatment for mucopolysaccharidosis II (MPS II), which is also called Hunter syndrome.

该子项目是利用 由NIH/NCRR资助的中心赠款提供的资源。子项目和 研究者（PI）可能从另一个NIH来源获得了主要资金， 因此可以在其他CRISP条目中表示。所列机构为 研究中心，而研究中心不一定是研究者所在的机构。 本研究的目的是继续测试实验酶艾杜糖醛酸-2-硫酸酯酶（I2 S）替代治疗粘多糖样变性II（MPS II）（也称为亨特氏综合征）的安全性和有效性。