MAINTENANCE STUDY OF IDURONATE-2-SULFATASE REPLACEMENT THERAPY IN MPS II PATIENT
MAINTENANCE STUDY OF IDURONATE-2-SULFATASE REPLACEMENT THERAPY IN MPS II PATIENT
批准号:
7625515
负责人:
JOSEPH J. MUENZER
金额:
$0.53万
依托单位国家:
美国
项目类别:
财政年份:
2006
资助国家:
美国
项目状态:
已结题
起止时间:
2006-12-01 至 2007-11-30
关键词:
Computer Retrieval of Information on Scientific Projects DatabaseEffectivenessEnzymesFundingGrantInstitutionMaintenanceMucopolysaccharidosis IIPatientsPurposeReplacement TherapyResearchResearch PersonnelResourcesSafetySourceTestingUnited States National Institutes of Healthiduronate-2-sulfataseresearch study
中文摘要
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英文摘要
This subproject is one of many research subprojects utilizing the
resources provided by a Center grant funded by NIH/NCRR. The subproject and
investigator (PI) may have received primary funding from another NIH source,
and thus could be represented in other CRISP entries. The institution listed is
for the Center, which is not necessarily the institution for the investigator.
The purpose of this research study is to continue to test the safety and effectiveness of the experimental enzyme, iduronate-2-sulfatase (I2S) replacement treatment for mucopolysaccharidosis II (MPS II), which is also called Hunter syndrome.
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TKT024EXT: MPS II PATIENTS RECEIVING IDURONATE-2-SULFATASE ENZYME REPLACEMENT
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批准号:7716800
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项目类别:
-
资助金额:$0.13万
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财政年份:2008
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负责人:JOSEPH J. MUENZER
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依托单位:
CLINICAL TRIAL: MAINTENANCE STUDY OF IDURONATE-2-SULFATASE REPLACEMENT THERAPY I
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批准号:7716755
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项目类别:
-
资助金额:$0.02万
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财政年份:2008
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负责人:JOSEPH J. MUENZER
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依托单位:
TKT024EXT: MPS II PATIENTS RECEIVING IDURONATE-2-SULFATASE ENZYME REPLACEMENT
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批准号:7625579
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项目类别:
-
资助金额:$2.25万
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财政年份:2006
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负责人:JOSEPH J. MUENZER
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依托单位:
MAINTENANCE STUDY OF IDURONATE-2-SULFATASE REPLACEMENT THERAPY IN MPS II PATIENT
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批准号:7377421
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项目类别:
-
资助金额:$0.89万
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财政年份:2005
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负责人:JOSEPH J. MUENZER
-
依托单位:
TKT024EXT: MPS II PATIENTS RECEIVING IDURONATE-2-SULFATASE ENZYME REPLACEMENT
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批准号:7377529
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项目类别:
-
资助金额:$8.08万
-
财政年份:2005
-
负责人:JOSEPH J. MUENZER
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依托单位:
BI-WEEKLY DOSING REGIMENS OF IDURONATE-2-SULFATASE ENZYME REPLACEMENT MPS II
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批准号:7377468
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项目类别:
-
资助金额:$1.39万
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财政年份:2005
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负责人:JOSEPH J. MUENZER
-
依托单位:
MAINTENANCE STUDY OF IDURONATE-2-SULFATASE REPLACEMENT THERAPY IN MPS II PATIENT
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批准号:7200214
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项目类别:
-
资助金额:$2.76万
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财政年份:2004
-
负责人:JOSEPH J. MUENZER
-
依托单位:
TKT024EXT: MPS II PATIENTS RECEIVING IDURONATE-2-SULFATASE ENZYME REPLACEMENT
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批准号:7200330
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项目类别:
-
资助金额:$0.28万
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财政年份:2004
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负责人:JOSEPH J. MUENZER
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依托单位:
BI-WEEKLY DOSING REGIMENS OF IDURONATE-2-SULFATASE ENZYME REPLACEMENT MPS II
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批准号:7200278
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项目类别:
-
资助金额:$18.54万
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财政年份:2004
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负责人:JOSEPH J. MUENZER
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依托单位:
MPS II: Validation of Childhood Health Assessment Questionnaire
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批准号:6980721
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项目类别:
-
资助金额:$0.11万
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财政年份:2003
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负责人:JOSEPH J. MUENZER
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依托单位:
Maintenance Study of Iduronate-2-Sulfatase Replacement Therapy in MPS II Patient
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批准号:6980643
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项目类别:
-
资助金额:$8.26万
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财政年份:2003
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负责人:JOSEPH J. MUENZER
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依托单位:
Bi-Weekly Dosing Regimens of Iduronate-2-Sulfatase Enzyme Replacement MPS II
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批准号:6980716
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项目类别:
-
资助金额:$2.18万
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财政年份:2003
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负责人:JOSEPH J. MUENZER
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依托单位:
ENZYME REPLACEMENT THERAPY FOR PATIENT W/ MUCOPOLYSACCHARIDOSIS I
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批准号:6566103
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项目类别:
-
资助金额:$19.07万
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财政年份:2001
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负责人:JOSEPH J. MUENZER
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依托单位:
ENZYME REPLACEMENT THERAPY FOR PATIENT W/ MUCOPOLYSACCHARIDOSIS I
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批准号:6504251
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项目类别:
-
资助金额:$19.07万
-
财政年份:2000
-
负责人:JOSEPH J. MUENZER
-
依托单位:
ENZYME REPLACEMENT THERAPY FOR PATIENT W/ MUCOPOLYSACCHARIDOSIS I
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批准号:6423274
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项目类别:
-
资助金额:$29.46万
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财政年份:2000
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负责人:JOSEPH J. MUENZER
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依托单位:
ENZYME REPLACEMENT THERAPY FOR PATIENT W/ MUCOPOLYSACCHARIDOSIS I
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批准号:6303934
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项目类别:
-
资助金额:$0.02万
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财政年份:1999
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负责人:JOSEPH J. MUENZER
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依托单位:
ENZYME REPLACEMENT THERAPY FOR PATIENT W/ MUCOPOLYSACCHARIDOSIS I
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批准号:6263894
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项目类别:
-
资助金额:$0.02万
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财政年份:1998
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负责人:JOSEPH J. MUENZER
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依托单位:
ENZYME REPLACEMENT THERAPY FOR PATIENT W/ MUCOPOLYSACCHARIDOSIS I
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批准号:6297262
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项目类别:
-
资助金额:$0.02万
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财政年份:1998
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负责人:JOSEPH J. MUENZER
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依托单位:
MOLECULAR GENETICS OF IDURONATE SULFATASE DEFICIENCIES
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批准号:3462552
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项目类别:
-
资助金额:$10.51万
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财政年份:1987
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负责人:JOSEPH J. MUENZER
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依托单位:
MOLECULAR GENETICS OF IDURONATE SULFATASE DEFICIENCIES
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批准号:3462553
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项目类别:
-
资助金额:$10.73万
-
财政年份:1987
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负责人:JOSEPH J. MUENZER
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依托单位:
海外基金