Rare Dis Clin Res Consortia (RDCRC) for Rare Dis Clin Res Network (U54)

罕见疾病临床研究联盟 (RDCRC) 的罕见疾病临床研究网络 (U54)

• 批准号: 9145799
• 负责人: MICHIO HIRANO
• 金额: $ 16.27万
• 依托单位: COLUMBIA UNIVERSITY HEALTH SCIENCES
• 依托单位国家: 美国
• 财政年份: 2014
• 资助国家: 美国
• 起止时间: 2014-09-01 至 2019-08-31
• 项目状态: 已结题
• 来源: https://reporter.nih.gov/project-details/9145799
• 关键词: Accident and Emergency department; Clinic; Clinical; Clinical Research; Clinical Trials; Clinical Trials Design; Colorado; Complex; Databases; Development; Diagnosis; Diagnostic; Educational process of instructing; Exposure to; Faculty; Fellowship; Fellowship Program; Florida; Generations; Heterogeneity; Institution; Instruction; K-Series Research Career Programs; Medical; Medicine; Metabolic Diseases; Mitochondria; Mitochondrial Diseases; Molecular; Patients; Research; Research Personnel; Research Training; Scientist; Site; Specialist; Telemedicine; Training; Training Programs; Universities; Visit; Writing; body system; data sharing; design; experience; interest; novel; professor; programs; symposium; training opportunity; translational medicine

The NAMDC Fellowship Program offers a unique training opportunity to senior postdoctoral clinical fellows who we anticipate will move on to the attending/assistant professor level in an academic setting as well-trained clinician scientists. The focus remains on translational medicine, teaching of diagnostic expertise and the development of clinical trials expertise. We aim to train the first of a new generation of clinician scientists who will be well equipped to move the promising new treatments for mitochondrial disease into the clinical arena. We plan to expand the program from seven training sites to nine. Our current sites include; Columbia, San Diego, Seattle, Cleveland, Hamilton, CHOP, and University of Florida. In this proposal we wish to add Baylor and University of Colorado at Denver. All are leading institutions in the new field of mitochondrial medicine. Each site brings a novel set of training experiences. World renowned faculty are to be found at each site. The initial exposure to mitochondrial patients, diagnosis and treatment will be provided during 3 to 6 months at UCSD in the Mitochondrial and Metabolic Disease Center. In this period an intensive clinical trials training program is required through the CREST program. Fellows will then choose to visit two or more consortium sites for periods from 1 to 3 months where a rich and varied training experience will be provided. The program will continue to be held together by regular telemedicine WebEx conferences involving all consortium sites. Data sharing is underway at all sites through the NAMDC database which the fellows will be actively involved with both at the patient entry level and analytically. At the end of their training the fellows will be encouraged to write a K award application.

NAMDC奖学金计划为高级博士后临床研究员提供了独特的培训机会 我们预计谁将在学术环境中接受良好的培训， 临床科学家。重点仍然是转化医学，诊断专业知识的教学 以及临床试验专业知识的发展。我们的目标是培养新一代临床医生中的第一批 科学家们将装备精良，将有希望的线粒体疾病新疗法， 临床竞技场。我们计划将该计划从7个培训地点扩大到9个。我们目前的网站 包括：哥伦比亚、圣地亚哥、西雅图、克利夫兰、汉密尔顿、CHOP和佛罗里达大学。在这 我们希望增加贝勒大学和丹佛的科罗拉多大学。所有这些都是新的领先机构 线粒体医学领域。每个网站都提供了一套新颖的培训体验。世界知名的教师 在每个站点都可以找到。最初接触线粒体的患者，诊断和治疗将 在加州大学圣地亚哥分校线粒体和代谢疾病中心提供3至6个月的时间。这一时期 一个密集的临床试验培训计划是需要通过CREST计划。研究员们将 选择访问两个或更多的财团网站，为期1至3个月，在那里进行丰富多样的培训 将提供经验。该计划将继续通过定期的远程医疗WebEx举行 涉及所有联合体地点的会议。通过NAMDC在所有站点共享数据 数据库，研究员将积极参与患者入门级和分析。在 在培训结束时，将鼓励研究员撰写K奖申请书。