CYSTEAMINE BITARTRATE DELAYED-RELESEASE CAPSULES (RP103) COMPARED TO CYSTEAMINE
CYSTEAMINE BITARTRATE DELAYED-RELESEASE CAPSULES (RP103) COMPARED TO CYSTEAMINE
批准号:
8166878
负责人:
BRUCE A BARSHOP
金额:
$1.95万
依托单位国家:
美国
项目类别:
财政年份:
2009
资助国家:
美国
项目状态:
已结题
起止时间:
2009-12-01 至 2010-06-30
中文摘要
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英文摘要
This subproject is one of many research subprojects utilizing the
resources provided by a Center grant funded by NIH/NCRR. The subproject and
investigator (PI) may have received primary funding from another NIH source,
and thus could be represented in other CRISP entries. The institution listed is
for the Center, which is not necessarily the institution for the investigator.
Asses the PK, PD, safety and tolerability of RP103 compared to Cystagon in patients with nephropathic cystinosis. Patients taking Cystagon as part of their treatment for cystinosis will be enrolled into the study and results will be used to inform the design the confirmatory PK and pivotal PD study comparing RP103 to Cystagon.
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CLINICAL TRIAL: A PHASE II STUDY OF PN401 PYRIMIDINE RESPONSIVE SYNDROME OF NEUR
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批准号:8166786
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项目类别:
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资助金额:$0.05万
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财政年份:2009
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负责人:BRUCE A BARSHOP
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依托单位:
CLINICAL TRIAL: ALGLUCOSIDASE ALFA TEMPORARY ACCESS PROGRAM (ATAP) PROTOCOL AGLU
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批准号:8166856
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项目类别:
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资助金额:$1.1万
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财政年份:2009
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负责人:BRUCE A BARSHOP
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依托单位:
CLINICAL TRIAL: A PHASE II STUDY OF PN401 PYRIMIDINE RESPONSIVE SYNDROME OF NEUR
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批准号:7950917
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项目类别:
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资助金额:$0.11万
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财政年份:2008
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负责人:BRUCE A BARSHOP
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依托单位:
CLINICAL TRIAL: MYOZYME? TEMPORARY ACCESS PROGRAM (MTAP)
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批准号:7951008
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项目类别:
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资助金额:$1.7万
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财政年份:2008
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负责人:BRUCE A BARSHOP
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依托单位:
CLINICAL TRIAL: EXTENSION STUDY - LATE ONSET POMPE DISEASE
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批准号:7950980
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项目类别:
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资助金额:$0.68万
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财政年份:2008
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负责人:BRUCE A BARSHOP
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依托单位:
CLINICAL TRIAL: EXTENSION STUDY - LATE ONSET POMPE DISEASE
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批准号:7724970
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项目类别:
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资助金额:$0.82万
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财政年份:2007
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负责人:BRUCE A BARSHOP
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依托单位:
CLINICAL TRIAL: MYOZYME TREATMENT IN PATIENTS WITH LATE ONSET POMPE DISEASE
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批准号:7724952
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项目类别:
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资助金额:$1.1万
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财政年份:2007
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负责人:BRUCE A BARSHOP
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依托单位:
CLINICAL TRIAL: A PHASE II STUDY OF PN401 PYRIMIDINE RESPONSIVE SYNDROME OF NEUR
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批准号:7724883
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项目类别:
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资助金额:$0.14万
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财政年份:2007
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负责人:BRUCE A BARSHOP
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依托单位:
PHASE II OPEN TRIAL OF DICHLOROACETATE IN CONGENITAL LACTIC ACIDEMIA
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批准号:7374170
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项目类别:
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资助金额:$0.26万
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财政年份:2006
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负责人:BRUCE A BARSHOP
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依托单位:
LEUCINE METABOLISM AND LIVER TRANSPLANTATION
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批准号:7374198
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项目类别:
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资助金额:$0.16万
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财政年份:2006
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负责人:BRUCE A BARSHOP
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依托单位:
MYOZYME TREATMENT IN PATIENTS WITH LATE ONSET POMPE DISEASE
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批准号:7606598
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项目类别:
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资助金额:$0.27万
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财政年份:2006
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负责人:BRUCE A BARSHOP
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依托单位:
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批准号:7374144
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项目类别:
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资助金额:$0.26万
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财政年份:2006
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负责人:BRUCE A BARSHOP
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依托单位:
A PHASE II STUDY OF PN401 PYRIMIDINE RESPONSIVE SYNDROME OF NEUROLOGICAL DYSF
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批准号:7606507
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项目类别:
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资助金额:$0.19万
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财政年份:2006
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负责人:BRUCE A BARSHOP
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Dichloroacetate in Congenital Lacic Acidemia
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批准号:7045450
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项目类别:
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资助金额:$0.3万
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财政年份:2003
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负责人:BRUCE A BARSHOP
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依托单位:
PHASE II OPEN TRIAL OF DICHLOROACETATE IN CONGENITAL LACTIC ACIDEMIA
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批准号:7205618
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项目类别:
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资助金额:$0.24万
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财政年份:2003
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负责人:BRUCE A BARSHOP
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依托单位:
Pn401 In Patients with Pyrimidine Responsive Syndrome
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批准号:7045386
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项目类别:
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资助金额:$0.35万
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财政年份:2003
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负责人:BRUCE A BARSHOP
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依托单位:
PN401 IN PATIENTS WITH PYRIMIDINE RESPONSIVE SYNDROME
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批准号:7205568
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项目类别:
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资助金额:$0.24万
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财政年份:2003
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负责人:BRUCE A BARSHOP
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依托单位:
DICHLOROACETATE IN THE TREATMENT OF CONGENITAL LACTIC ACIDEMIA
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批准号:7205571
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资助金额:$0.12万
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财政年份:2003
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负责人:BRUCE A BARSHOP
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依托单位:
LEUCINE METABOLISM AND LIVER TRANSPLANTATION
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项目类别:
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资助金额:$0.85万
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财政年份:2003
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负责人:BRUCE A BARSHOP
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HOMOCYSTEINE METABOLISM IN VASCULAR DISEASE
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项目类别:
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资助金额:$1.64万
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