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CLINICAL TRIAL: EXTENSION STUDY - LATE ONSET POMPE DISEASE

CLINICAL TRIAL: EXTENSION STUDY - LATE ONSET POMPE DISEASE
临床试验：扩展研究 - 迟发性庞贝病
批准号：
7724970
负责人：
BRUCE A BARSHOP
金额：
$0.82万
依托单位：
UNIVERSITY OF CALIFORNIA, SAN DIEGO
依托单位国家：
美国
项目类别：
财政年份：
2007
资助国家：
美国
项目状态：
已结题
起止时间：
2007-12-01 至 2008-11-30
来源：
https://reporter.nih.gov/project-details/7724970
关键词：
Clinical TrialsComputer Retrieval of Information on Scientific Projects DatabaseDouble-Blind MethodFundingGlycogen storage disease type IIGrantInstitutionOrphan DiseasePatientsPlacebo ControlResearchResearch PersonnelResourcesSafetySourceUnited States National Institutes of Health

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中文摘要
翻译
这个子项目是众多研究子项目之一
英文摘要
This subproject is one of many research subprojects utilizing the resources provided by a Center grant funded by NIH/NCRR. The subproject and investigator (PI) may have received primary funding from another NIH source, and thus could be represented in other CRISP entries. The institution listed is for the Center, which is not necessarily the institution for the investigator. Assess the long term safety and efficacy of Myozyme treatment in patients with late onset Pompe disease who were previously treated under the placebo-controlled, double blind study AGLU02704. Orphan disease status.
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