课题基金 / 基金详情

MYOZYME TREATMENT IN PATIENTS WITH LATE ONSET POMPE DISEASE

MYOZYME TREATMENT IN PATIENTS WITH LATE ONSET POMPE DISEASE
Myozyme 治疗晚发性庞贝病患者
批准号:
7606598
负责人:
BRUCE A BARSHOP
金额:
$0.27万
依托单位国家:
美国
项目类别:
财政年份:
2006
资助国家:
美国
项目状态:
已结题
起止时间:
2006-12-01 至 2007-11-30

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项目成果

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中文摘要
翻译
该子项目是利用 由NIH/NCRR资助的中心赠款提供的资源。子项目和 研究者(PI)可能从另一个NIH来源获得主要资金, 因此可以在其他CRISP条目中表示。列出的机构是 中心,不一定是研究者的机构。 评价美而赞治疗与安慰剂相比在晚发型庞贝氏症患者中的安全性、疗效和PK。
英文摘要
This subproject is one of many research subprojects utilizing the resources provided by a Center grant funded by NIH/NCRR. The subproject and investigator (PI) may have received primary funding from another NIH source, and thus could be represented in other CRISP entries. The institution listed is for the Center, which is not necessarily the institution for the investigator. Evaluate the safety, efficacy and PK of Myozyme treatment in patients with late onset Pompe disease compared to placebo.
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