MYOZYME TREATMENT IN PATIENTS WITH LATE ONSET POMPE DISEASE
MYOZYME TREATMENT IN PATIENTS WITH LATE ONSET POMPE DISEASE
批准号:
7606598
负责人:
BRUCE A BARSHOP
金额:
$0.27万
依托单位国家:
美国
项目类别:
财政年份:
2006
资助国家:
美国
项目状态:
已结题
起止时间:
2006-12-01 至 2007-11-30
中文摘要
该子项目是利用
由NIH/NCRR资助的中心赠款提供的资源。子项目和
研究者(PI)可能从另一个NIH来源获得主要资金,
因此可以在其他CRISP条目中表示。列出的机构是
中心,不一定是研究者的机构。
评价美而赞治疗与安慰剂相比在晚发型庞贝氏症患者中的安全性、疗效和PK。
英文摘要
This subproject is one of many research subprojects utilizing the
resources provided by a Center grant funded by NIH/NCRR. The subproject and
investigator (PI) may have received primary funding from another NIH source,
and thus could be represented in other CRISP entries. The institution listed is
for the Center, which is not necessarily the institution for the investigator.
Evaluate the safety, efficacy and PK of Myozyme treatment in patients with late onset Pompe disease compared to placebo.
期刊论文(0)
专著(0)
科研奖励(0)
会议论文
CYSTEAMINE BITARTRATE DELAYED-RELESEASE CAPSULES (RP103) COMPARED TO CYSTEAMINE
-
批准号:8166878
-
项目类别:
-
资助金额:$1.95万
-
财政年份:2009
-
负责人:BRUCE A BARSHOP
-
依托单位:
CLINICAL TRIAL: A PHASE II STUDY OF PN401 PYRIMIDINE RESPONSIVE SYNDROME OF NEUR
-
批准号:8166786
-
项目类别:
-
资助金额:$0.05万
-
财政年份:2009
-
负责人:BRUCE A BARSHOP
-
依托单位:
CLINICAL TRIAL: ALGLUCOSIDASE ALFA TEMPORARY ACCESS PROGRAM (ATAP) PROTOCOL AGLU
-
批准号:8166856
-
项目类别:
-
资助金额:$1.1万
-
财政年份:2009
-
负责人:BRUCE A BARSHOP
-
依托单位:
CLINICAL TRIAL: A PHASE II STUDY OF PN401 PYRIMIDINE RESPONSIVE SYNDROME OF NEUR
-
批准号:7950917
-
项目类别:
-
资助金额:$0.11万
-
财政年份:2008
-
负责人:BRUCE A BARSHOP
-
依托单位:
CLINICAL TRIAL: MYOZYME? TEMPORARY ACCESS PROGRAM (MTAP)
-
批准号:7951008
-
项目类别:
-
资助金额:$1.7万
-
财政年份:2008
-
负责人:BRUCE A BARSHOP
-
依托单位:
CLINICAL TRIAL: EXTENSION STUDY - LATE ONSET POMPE DISEASE
-
批准号:7950980
-
项目类别:
-
资助金额:$0.68万
-
财政年份:2008
-
负责人:BRUCE A BARSHOP
-
依托单位:
CLINICAL TRIAL: EXTENSION STUDY - LATE ONSET POMPE DISEASE
-
批准号:7724970
-
项目类别:
-
资助金额:$0.82万
-
财政年份:2007
-
负责人:BRUCE A BARSHOP
-
依托单位:
CLINICAL TRIAL: MYOZYME TREATMENT IN PATIENTS WITH LATE ONSET POMPE DISEASE
-
批准号:7724952
-
项目类别:
-
资助金额:$1.1万
-
财政年份:2007
-
负责人:BRUCE A BARSHOP
-
依托单位:
CLINICAL TRIAL: A PHASE II STUDY OF PN401 PYRIMIDINE RESPONSIVE SYNDROME OF NEUR
-
批准号:7724883
-
项目类别:
-
资助金额:$0.14万
-
财政年份:2007
-
负责人:BRUCE A BARSHOP
-
依托单位:
PHASE II OPEN TRIAL OF DICHLOROACETATE IN CONGENITAL LACTIC ACIDEMIA
-
批准号:7374170
-
项目类别:
-
资助金额:$0.26万
-
财政年份:2006
-
负责人:BRUCE A BARSHOP
-
依托单位:
LEUCINE METABOLISM AND LIVER TRANSPLANTATION
-
批准号:7374198
-
项目类别:
-
资助金额:$0.16万
-
财政年份:2006
-
负责人:BRUCE A BARSHOP
-
依托单位:
A PHASE II STUDY OF PN401 PYRIMIDINE RESPONSIVE SYNDROME OF NEUROLOGICAL DYSF
-
批准号:7374144
-
项目类别:
-
资助金额:$0.26万
-
财政年份:2006
-
负责人:BRUCE A BARSHOP
-
依托单位:
A PHASE II STUDY OF PN401 PYRIMIDINE RESPONSIVE SYNDROME OF NEUROLOGICAL DYSF
-
批准号:7606507
-
项目类别:
-
资助金额:$0.19万
-
财政年份:2006
-
负责人:BRUCE A BARSHOP
-
依托单位:
Dichloroacetate in Congenital Lacic Acidemia
-
批准号:7045450
-
项目类别:
-
资助金额:$0.3万
-
财政年份:2003
-
负责人:BRUCE A BARSHOP
-
依托单位:
PHASE II OPEN TRIAL OF DICHLOROACETATE IN CONGENITAL LACTIC ACIDEMIA
-
批准号:7205618
-
项目类别:
-
资助金额:$0.24万
-
财政年份:2003
-
负责人:BRUCE A BARSHOP
-
依托单位:
Pn401 In Patients with Pyrimidine Responsive Syndrome
-
批准号:7045386
-
项目类别:
-
资助金额:$0.35万
-
财政年份:2003
-
负责人:BRUCE A BARSHOP
-
依托单位:
PN401 IN PATIENTS WITH PYRIMIDINE RESPONSIVE SYNDROME
-
批准号:7205568
-
项目类别:
-
资助金额:$0.24万
-
财政年份:2003
-
负责人:BRUCE A BARSHOP
-
依托单位:
DICHLOROACETATE IN THE TREATMENT OF CONGENITAL LACTIC ACIDEMIA
-
批准号:7205571
-
项目类别:
-
资助金额:$0.12万
-
财政年份:2003
-
负责人:BRUCE A BARSHOP
-
依托单位:
LEUCINE METABOLISM AND LIVER TRANSPLANTATION
-
批准号:7205661
-
项目类别:
-
资助金额:$0.85万
-
财政年份:2003
-
负责人:BRUCE A BARSHOP
-
依托单位:
HOMOCYSTEINE METABOLISM IN VASCULAR DISEASE
-
批准号:6249115
-
项目类别:
-
资助金额:$1.64万
-
财政年份:1997
-
负责人:BRUCE A BARSHOP
-
依托单位:
海外基金