课题基金 / 基金详情

CLINICAL TRIAL: MYOZYME TREATMENT IN PATIENTS WITH LATE ONSET POMPE DISEASE

CLINICAL TRIAL: MYOZYME TREATMENT IN PATIENTS WITH LATE ONSET POMPE DISEASE
临床试验:MYOZYME 治疗晚发性庞贝病患者
批准号:
7724952
负责人:
BRUCE A BARSHOP
金额:
$1.1万
依托单位国家:
美国
项目类别:
财政年份:
2007
资助国家:
美国
项目状态:
已结题
起止时间:
2007-12-01 至 2008-11-30

项目摘要

项目成果

BRUCE A BARSHOP的其他基金

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中文摘要
翻译
这个子项目是许多研究子项目中的一个 由NIH/NCRR资助的中心赠款提供的资源。子项目和 研究者(PI)可能从另一个NIH来源获得了主要资金, 因此可以在其他CRISP条目中表示。所列机构为 中心,不一定是研究者的机构。 评价美而赞治疗与安慰剂相比在晚发型庞贝氏症患者中的安全性、疗效和PK。
英文摘要
This subproject is one of many research subprojects utilizing the resources provided by a Center grant funded by NIH/NCRR. The subproject and investigator (PI) may have received primary funding from another NIH source, and thus could be represented in other CRISP entries. The institution listed is for the Center, which is not necessarily the institution for the investigator. Evaluate the safety, efficacy and PK of Myozyme treatment in patients with late onset Pompe disease compared to placebo.
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